Assessment of Therapeutic Potential of a Dual AAV Approach for Duchenne Muscular Dystrophy

por Albini, Sonia, Palmieri, Laura, Dubois, Auriane, Bourg, Nathalie, Lostal, William, Richard, Isabelle
Publicado 2023

A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence

por Pryadkina, Marina, Lostal, William, Bourg, Nathalie, Charton, Karine, Roudaut, Carinne, Hirsch, Matthew L, Richard, Isabelle
Publicado 2015

Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies

por Israeli, David, Poupiot, Jérôme, Amor, Fatima, Charton, Karine, Lostal, William, Jeanson-Leh, Laurence, Richard, Isabelle
Publicado 2016

Co-Administration of Simvastatin Does Not Potentiate the Benefit of Gene Therapy in the mdx Mouse Model for Duchenne Muscular Dystrophy

por Bourg, Nathalie, Vu Hong, Ai, Lostal, William, Jaber, Abbass, Guerchet, Nicolas, Tanniou, Guillaume, Bordier, Fanny, Bertil-Froidevaux, Emilie, Georger, Christophe, Daniele, Nathalie, Richard, Isabelle, Israeli, David
Publicado 2022

Lack of Correlation between Outcomes of Membrane Repair Assay and Correction of Dystrophic Changes in Experimental Therapeutic Strategy in Dysferlinopathy

por Lostal, William, Bartoli, Marc, Roudaut, Carinne, Bourg, Nathalie, Krahn, Martin, Pryadkina, Marina, Borel, Perrine, Suel, Laurence, Roche, Joseph A., Stockholm, Daniel, Bloch, Robert J., Levy, Nicolas, Bashir, Rumaisa, Richard, Isabelle
Publicado 2012