Relative persistence of AAV serotype 1 vector genomes in dystrophic muscle

por Pacak, Christina A, Conlon, Thomas, Mah, Cathryn S, Byrne, Barry J
Publicado 2008

Tissue specific promoters improve specificity of AAV9 mediated transgene expression following intra-vascular gene delivery in neonatal mice

por Pacak, Christina A, Sakai, Yoshihisa, Thattaliyath, Bijoy D, Mah, Cathryn S, Byrne, Barry J
Publicado 2008

Tissue specific promoters improve specificity of AAV9 mediated transgene expression following intra-vascular gene delivery in neonatal mice

por Pacak, Christina A, Sakai, Yoshihisa, Thattaliyath, Bijoy D, Mah, Cathryn S, Byrne, Barry J
Publicado 2009

Comparative impact of AAV and enzyme replacement therapy on respiratory and cardiac function in adult Pompe mice

por Falk, Darin J, Soustek, Meghan S, Todd, Adrian Gary, Mah, Cathryn S, Cloutier, Denise A, Kelley, Jeffry S, Clement, Nathalie, Fuller, David D, Byrne, Barry J
Publicado 2015

Glycogen Storage Disease Type Ia in Canines: A Model for Human Metabolic and Genetic Liver Disease

por Specht, Andrew, Fiske, Laurie, Erger, Kirsten, Cossette, Travis, Verstegen, John, Campbell-Thompson, Martha, Struck, Maggie B., Lee, Young Mok, Chou, Janice Y., Byrne, Barry J., Correia, Catherine E., Mah, Cathryn S., Weinstein, David A., Conlon, Thomas J.
Publicado 2011