Improved growth of a child with primary distal renal tubular acidosis after switching from a conventional alkalizing treatment to a new prolonged-release formulation containing pot...

por Boyer, Olivia, Manso-Silván, Maria A., Joukoff, Sophie, Berthaud, Romain, Guittet, Catherine
Publicado 2022

Lived experiences of patients with distal renal tubular acidosis treated with ADV7103 and of their caregivers: a qualitative study

por Acquadro, Michaël, Marrel, Alexia, Manso-Silván, Maria A., Guittet, Catherine, Joukoff, Sophie, Bertholet-Thomas, Aurélia
Publicado 2022

An innovative ethosuximide granule formulation designed for pediatric use: Comparative pharmacokinetics, safety, tolerability, and palatability profile versus reference syrup

por Diezi, Léonore, Dao, Kim, Jullien, Vincent, Roussel‐Maupetit, Caroline, Burton, Ingrid, André, Pascal, Bardinet, Carine, Rothuizen, Laura E., Chtioui, Haithem, Manso‐Silvan, Maria A., Guittet, Catherine, Brunner‐Ferber, Françoise, Vandenhende, Francois, Chiron, Catherine, Granier, Luc‐André, Buclin, Thierry
Publicado 2022

Efficacy and safety of an innovative prolonged-release combination drug in patients with distal renal tubular acidosis: an open-label comparative trial versus standard of care trea...

por Bertholet-Thomas, Aurélia, Guittet, Catherine, Manso-Silván, Maria A., Castang, Arnaud, Baudouin, Véronique, Cailliez, Mathilde, Di Maio, Massimo, Gillion-Boyer, Olivia, Golubovic, Emilija, Harambat, Jérôme, Klein, Alexandre, Knebelmann, Bertrand, Nobili, François, Novo, Robert, Podracka, Ludmila, Roussey-Kesler, Gwenaëlle, Stylianou, Christos, Granier, Luc-André
Publicado 2020

Safety, efficacy, and acceptability of ADV7103 during 24 months of treatment: an open-label study in pediatric and adult patients with distal renal tubular acidosis

por Bertholet-Thomas, Aurélia, Guittet, Catherine, Manso-Silván, Maria A., Joukoff, Sophie, Navas-Serrano, Victor, Baudouin, Véronique, Cailliez, Mathilde, Di Maio, Massimo, Gillion-Boyer, Olivia, Golubovic, Emilija, Harambat, Jérôme, Knebelmann, Bertrand, Nobili, François, Novo, Robert, Podracka, Ludmila, Roussey-Kesler, Gwenaëlle, Granier, Luc-André
Publicado 2021