Pharmacokinetic/Pharmacodynamic Modeling of a Cell-Penetrating Peptide Phosphorodiamidate Morpholino Oligomer in mdx Mice

por Mukashyaka, Marie Claire, Wu, Chia-Ling, Ha, Kristin, Zhang, Jianbo, Wood, Jenna, Foley, Samantha, Mastis, Bryan, Jungels, Nino, Sun, Huadong, Shadid, Mohammad, Harriman, Shawn, Hadcock, John R.
Publicado 2021

Widespread AAV1- and AAV2-mediated transgene expression in the nonhuman primate brain: implications for Huntington’s disease

por Hadaczek, Piotr, Stanek, Lisa, Ciesielska, Agnieszka, Sudhakar, Vivek, Samaranch, Lluis, Pivirotto, Philip, Bringas, John, O’Riordan, Catherine, Mastis, Bryan, San Sebastian, Waldy, Forsayeth, John, Cheng, Seng H, Bankiewicz, Krystof S, Shihabuddin, Lamya S
Publicado 2016