Interactions between Retroviruses and the Host Cell Genome

por Poletti, Valentina, Mavilio, Fulvio
Publicado 2017

Gene Therapy for Hemoglobinopathies

por Cavazzana, Marina, Mavilio, Fulvio
Publicado 2018

Designing Lentiviral Vectors for Gene Therapy of Genetic Diseases

por Poletti, Valentina, Mavilio, Fulvio
Publicado 2021

The Pharmacology of Gene and Cell Therapy

por Conlon, Thomas J., Mavilio, Fulvio
Publicado 2018

Ex Vivo COL7A1 Correction for Recessive Dystrophic Epidermolysis Bullosa Using CRISPR/Cas9 and Homology-Directed Repair

por Izmiryan, Araksya, Ganier, Clarisse, Bovolenta, Matteo, Schmitt, Alain, Mavilio, Fulvio, Hovnanian, Alain
Publicado 2018

C/EBPδ regulates cell cycle and self-renewal of human limbal stem cells

por Barbaro, Vanessa, Testa, Anna, Di Iorio, Enzo, Mavilio, Fulvio, Pellegrini, Graziella, De Luca, Michele
Publicado 2007

The GATA1-HS2 Enhancer Allows Persistent and Position-Independent Expression of a β-globin Transgene

por Miccio, Annarita, Poletti, Valentina, Tiboni, Francesca, Rossi, Claudia, Antonelli, Antonella, Mavilio, Fulvio, Ferrari, Giuliana
Publicado 2011

Estimated Comparative Integration Hotspots Identify Different Behaviors of Retroviral Gene Transfer Vectors

por Ambrosi, Alessandro, Glad, Ingrid K., Pellin, Danilo, Cattoglio, Claudia, Mavilio, Fulvio, Di Serio, Clelia, Frigessi, Arnoldo
Publicado 2011

Transcription Factor Binding Sites Are Genetic Determinants of Retroviral Integration in the Human Genome

por Felice, Barbara, Cattoglio, Claudia, Cittaro, Davide, Testa, Anna, Miccio, Annarita, Ferrari, Giuliana, Luzi, Lucilla, Recchia, Alessandra, Mavilio, Fulvio
Publicado 2009

Genome-Wide Analysis of Alpharetroviral Integration in Human Hematopoietic Stem/Progenitor Cells

por Moiani, Arianna, Suerth, Julia Debora, Gandolfi, Francesco, Rizzi, Ermanno, Severgnini, Marco, De Bellis, Gianluca, Schambach, Axel, Mavilio, Fulvio
Publicado 2014

Genomic Analysis of Sleeping Beauty Transposon Integration in Human Somatic Cells

por Turchiano, Giandomenico, Latella, Maria Carmela, Gogol-Döring, Andreas, Cattoglio, Claudia, Mavilio, Fulvio, Izsvák, Zsuzsanna, Ivics, Zoltán, Recchia, Alessandra
Publicado 2014

Correction: Genomic Analysis of Sleeping Beauty Transposon Integration in Human Somatic Cells

por Turchiano, Giandomenico, Latella, Maria Carmela, Döring, Andreas Gogol, Cattoglio, Claudia, Mavilio, Fulvio, Izsvák, Zsuzsanna, Ivics, Zoltán, Recchia, Alessandra
Publicado 2020

Deletion of the LTR Enhancer/Promoter Has No Impact on the Integration Profile of MLV Vectors in Human Hematopoietic Progenitors

por Moiani, Arianna, Miccio, Annarita, Rizzi, Ermanno, Severgnini, Marco, Pellin, Danilo, Suerth, Julia Debora, Baum, Christopher, De Bellis, Gianluca, Mavilio, Fulvio
Publicado 2013

Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System

por Lattanzi, Annalisa, Duguez, Stephanie, Moiani, Arianna, Izmiryan, Araksya, Barbon, Elena, Martin, Samia, Mamchaoui, Kamel, Mouly, Vincent, Bernardi, Francesco, Mavilio, Fulvio, Bovolenta, Matteo
Publicado 2017

Genome-wide analysis of promoter and enhancer usage in hematopoietic stem cell differentiation

por Miccio, Annarita, Peano, Clelia, Romano, Oriana, Tagliazucchi, Guidantonio, Petiti, Luca, Cifola, Ingrid, Rizzi, Ermanno, Severgnini, Marco, Bicciato, Silvio, De Bellis, Gianluca, Mavilio, Fulvio
Publicado 2013

Dynamic Transcriptional and Epigenetic Regulation of Human Epidermal Keratinocyte Differentiation

por Cavazza, Alessia, Miccio, Annarita, Romano, Oriana, Petiti, Luca, Malagoli Tagliazucchi, Guidantonio, Peano, Clelia, Severgnini, Marco, Rizzi, Ermanno, De Bellis, Gianluca, Bicciato, Silvio, Mavilio, Fulvio
Publicado 2016

Preclinical Development of a Lentiviral Vector for Gene Therapy of X-Linked Severe Combined Immunodeficiency

por Poletti, Valentina, Charrier, Sabine, Corre, Guillaume, Gjata, Bernard, Vignaud, Alban, Zhang, Fang, Rothe, Michael, Schambach, Axel, Gaspar, H. Bobby, Thrasher, Adrian J., Mavilio, Fulvio
Publicado 2018

Pre-clinical Development of a Lentiviral Vector Expressing the Anti-sickling βAS3 Globin for Gene Therapy for Sickle Cell Disease

por Poletti, Valentina, Urbinati, Fabrizia, Charrier, Sabine, Corre, Guillaume, Hollis, Roger P., Campo Fernandez, Beatriz, Martin, Samia, Rothe, Michael, Schambach, Axel, Kohn, Donald B., Mavilio, Fulvio
Publicado 2018

Nup153 and Nup98 bind the HIV-1 core and contribute to the early steps of HIV-1 replication

por Di Nunzio, Francesca, Fricke, Thomas, Miccio, Annarita, Valle-Casuso, Jose Carlos, Perez, Patricio, Souque, Philippe, Rizzi, Ermanno, Severgnini, Marco, Mavilio, Fulvio, Charneau, Pierre, Diaz-Griffero, Felipe
Publicado 2013

Efficacy and biodistribution analysis of intracerebroventricular administration of an optimized scAAV9-SMN1 vector in a mouse model of spinal muscular atrophy

por Armbruster, Nicole, Lattanzi, Annalisa, Jeavons, Matthieu, Van Wittenberghe, Laetitia, Gjata, Bernard, Marais, Thibaut, Martin, Samia, Vignaud, Alban, Voit, Thomas, Mavilio, Fulvio, Barkats, Martine, Buj-Bello, Ana
Publicado 2016