Animal models of β-hemoglobinopathies: utility and limitations

por McColl, Bradley, Vadolas, Jim
Publicado 2016

The therapeutic potential of genome editing for β-thalassemia

por Glaser, Astrid, McColl, Bradley, Vadolas, Jim
Publicado 2015

GFP to BFP Conversion: A Versatile Assay for the Quantification of CRISPR/Cas9-mediated Genome Editing

por Glaser, Astrid, McColl, Bradley, Vadolas, Jim
Publicado 2016

An intronic mutation in Chd7 creates a cryptic splice site, causing aberrant splicing in a mouse model of CHARGE syndrome

por Ogier, Jacqueline M., Arhatari, Benedicta D., Carpinelli, Marina R., McColl, Bradley K., Wilson, Michael A., Burt, Rachel A.
Publicado 2018

A Cas9 Variant for Efficient Generation of Indel-Free Knockin or Gene-Corrected Human Pluripotent Stem Cells

por Howden, Sara E., McColl, Bradley, Glaser, Astrid, Vadolas, Jim, Petrou, Steven, Little, Melissa H., Elefanty, Andrew G., Stanley, Edouard G.
Publicado 2016

Plasmin Activates the Lymphangiogenic Growth Factors VEGF-C and VEGF-D

por McColl, Bradley K., Baldwin, Megan E., Roufail, Sally, Freeman, Craig, Moritz, Robert L., Simpson, Richard J., Alitalo, Kari, Stacker, Steven A., Achen, Marc G.
Publicado 2003

Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia

por Nualkaew, Tiwaporn, Sii-Felice, Karine, Giorgi, Marie, McColl, Bradley, Gouzil, Julie, Glaser, Astrid, Voon, Hsiao P.J., Tee, Hsin Y., Grigoriadis, George, Svasti, Saovaros, Fucharoen, Suthat, Hongeng, Suradej, Leboulch, Philippe, Payen, Emmanuel, Vadolas, Jim
Publicado 2021