Hemophilia A gene therapy via intraosseous delivery of factor VIII-lentiviral vectors

por Miao, Carol H.
Publicado 2016

The dataset from administration of single or combined immunomodulation agents to modulate anti-FVIII antibody responses in FVIII plasmid or protein primed hemophilia A mice

por Liu, Chao Lien, Lyle, Meghan J., Shin, Simon C., Miao, Carol H.
Publicado 2016

Anti-CD20 as the B-Cell Targeting Agent in a Combined Therapy to Modulate Anti-Factor VIII Immune Responses in Hemophilia a Inhibitor Mice

por Liu, Chao Lien, Ye, Peiqing, Lin, Jacqueline, Butts, Chérie L., Miao, Carol H.
Publicado 2014

A Treg-Selective IL-2 Mutein Prevents the Formation of Factor VIII Inhibitors in Hemophilia Mice Treated With Factor VIII Gene Therapy

por Chen, Alex C., Cai, Xiaohe, Li, Chong, Khoryati, Liliane, Gavin, Marc A., Miao, Carol H.
Publicado 2020

Effect of chimeric antigen receptor T cells against protease-activated receptor 1 for treating pancreatic cancer

por Hung, Hao-Chien, Fan, Ming-Huei, Wang, Daniel, Miao, Carol H., Su, Pong, Liu, Chao-Lien
Publicado 2023

Ex Vivo Expanded Human Vγ9Vδ2 T-Cells Can Suppress Epithelial Ovarian Cancer Cell Growth

por Mao, Tsui Lien, Miao, Carol H., Liao, Yi Jen, Chen, Ying Jen, Yeh, Chia Yu, Liu, Chao Lien
Publicado 2019

Engineering Chimeric Antigen Receptor T Cells against Immune Checkpoint Inhibitors PD-1/PD-L1 for Treating Pancreatic Cancer

por Yang, Ching-Yao, Fan, Ming Huei, Miao, Carol H., Liao, Yi Jen, Yuan, Ray-Hwang, Liu, Chao Lien
Publicado 2020

Induction of long-term tolerance to a specific antigen using anti-CD3 lipid nanoparticles following gene therapy

por Chen, Chun-Yu, Vander Kooi, Amber, Cavedon, Alex, Cai, Xiaohe, Hoggatt, Jonathan, Martini, Paolo G.V., Miao, Carol H.
Publicado 2023

Site-Specific N- and O-Glycosylation Analysis of Human Plasma Fibronectin

por Liu, Ding, Wang, Shuaishuai, Zhang, Junping, Xiao, Weidong, Miao, Carol H., Konkle, Barbara A., Wan, Xiu-Feng, Li, Lei
Publicado 2021

Transcutaneous Ultrasound-Mediated Nonviral Gene Delivery to the Liver in a Porcine Model

por Tran, Dominic M., Zhang, Feng, Morrison, Kyle P., Loeb, Keith R., Harrang, James, Kajimoto, Masaki, Chavez, Francisco, Wu, Li, Miao, Carol H.
Publicado 2019

Treatment of Hemophilia A Using Factor VIII Messenger RNA Lipid Nanoparticles

por Chen, Chun-Yu, Tran, Dominic M., Cavedon, Alex, Cai, Xiaohe, Rajendran, Raj, Lyle, Meghan J., Martini, Paolo G.V., Miao, Carol H.
Publicado 2020

Ultrasound-mediated gene delivery of factor VIII plasmids for hemophilia A gene therapy in mice

por Song, Shuxian, Lyle, Meghan J., Noble-Vranish, Misty L., Min-Tran, Dominic M., Harrang, James, Xiao, Weidong, Unger, Evan C., Miao, Carol H.
Publicado 2022

Ultrasound-Mediated Gene Therapy in Swine Livers Using Single-Element, Multi-lensed, High-Intensity Ultrasound Transducers

por Noble-Vranish, Misty L., Song, Shuxian, Morrison, Kyle P., Tran, Dominic M., Sun, Ryan R., Loeb, Keith R., Keilman, George W., Miao, Carol H.
Publicado 2018

Intraosseous delivery of platelet-targeted factor VIII lentiviral vector in humanized NBSGW mice

por Joo, Julia H., Wang, Xuefeng, Singh, Swati, Chen, Chun-Yu, Li, Chong, Adair, Jennifer E., Kiem, Hans-Peter, Rawlings, David J., Miao, Carol H.
Publicado 2022

Comparative glycosylation mapping of plasma-derived and recombinant human factor VIII

por Qu, Jingyao, Ma, Cheng, Xu, Xiao-Qian, Xiao, Min, Zhang, Junping, Li, Dong, Liu, Ding, Konkle, Barbara A., Miao, Carol H., Li, Lei, Xiao, Weidong
Publicado 2020

Transcutaneous ultrasound-mediated gene delivery into canine livers achieves therapeutic levels of factor VIII expression

por Manson, Megan A., Zhang, Feng, Novokhodko, Alexander, Chen, Chun-Yu, Parker, Maura, Loeb, Keith R., Kajimoto, Masaki, Campbell, Carley, Storb, Rainer F., Miao, Carol H.
Publicado 2022

Engineering Protein-Secreting Plasma Cells by Homology-Directed Repair in Primary Human B Cells

por Hung, King L., Meitlis, Iana, Hale, Malika, Chen, Chun-Yu, Singh, Swati, Jackson, Shaun W., Miao, Carol H., Khan, Iram F., Rawlings, David J., James, Richard G.
Publicado 2018

Influence of N-glycosylation in the A and C domains on the immunogenicity of factor VIII

por Vander Kooi, Amber, Wang, Shuaishuai, Fan, Meng-Ni, Chen, Alex, Zhang, Junping, Chen, Chun-Yu, Cai, Xiaohe, Konkle, Barbara A., Xiao, Weidong, Li, Lei, Miao, Carol H.
Publicado 2022