Natural history study and statistical modeling of disease progression in a preclinical model of myotubular myopathy

por Buono, Suzie, Monseur, Arnaud, Menuet, Alexia, Robé, Anne, Koch, Catherine, Laporte, Jocelyn, Thielemans, Leen, Depla, Marion, Cowling, Belinda S.
Publicado 2022

Myostatin: a Circulating Biomarker Correlating with Disease in Myotubular Myopathy Mice and Patients

por Koch, Catherine, Buono, Suzie, Menuet, Alexia, Robé, Anne, Djeddi, Sarah, Kretz, Christine, Gomez-Oca, Raquel, Depla, Marion, Monseur, Arnaud, Thielemans, Leen, Servais, Laurent, Laporte, Jocelyn, Cowling, Belinda S.
Publicado 2020

Hierarchical Bayesian modelling of disease progression to inform clinical trial design in centronuclear myopathy

por Fouarge, Eve, Monseur, Arnaud, Boulanger, Bruno, Annoussamy, Mélanie, Seferian, Andreea M., De Lucia, Silvana, Lilien, Charlotte, Thielemans, Leen, Paradis, Khazal, Cowling, Belinda S., Freitag, Chris, Carlin, Bradley P., Servais, Laurent
Publicado 2021