Adeno-Associated Viral Vector Serotype 5 Poorly Transduces Liver in Rat Models

por Montenegro-Miranda, Paula S., Pañeda, Astrid, ten Bloemendaal, Lysbeth, Duijst, Suzanne, de Waart, Dirk R., Aseguinolaza, Gloria Gonzalez, Bosma, Piter J.
Publicado 2013

Enhanced Factor IX Activity following Administration of AAV5-R338L “Padua” Factor IX versus AAV5 WT Human Factor IX in NHPs

por Spronck, Elisabeth A., Liu, Ying Poi, Lubelski, Jacek, Ehlert, Erich, Gielen, Sander, Montenegro-Miranda, Paula, de Haan, Martin, Nijmeijer, Bart, Ferreira, Valerie, Petry, Harald, van Deventer, Sander J.
Publicado 2019

Intrastriatal Administration of AAV5-miHTT in Non-Human Primates and Rats Is Well Tolerated and Results in miHTT Transgene Expression in Key Areas of Huntington Disease Pathology

por Spronck, Elisabeth A., Vallès, Astrid, Lampen, Margit H., Montenegro-Miranda, Paula S., Keskin, Sonay, Heijink, Liesbeth, Evers, Melvin M., Petry, Harald, van Deventer, Sander J., Konstantinova, Pavlina, de Haan, Martin
Publicado 2021

A Novel Organoid Model of Damage and Repair Identifies HNF4α as a Critical Regulator of Intestinal Epithelial Regeneration

por Montenegro-Miranda, Paula S., van der Meer, Jonathan H.M., Jones, Christine, Meisner, Sander, Vermeulen, Jacqueline L.M., Koster, Jan, Wildenberg, Manon E., Heijmans, Jarom, Boudreau, Francois, Ribeiro, Agnes, van den Brink, Gijs R., Muncan, Vanesa
Publicado 2020