Development of gene therapy: potential in severe combined immunodeficiency due to adenosine deaminase deficiency

por Montiel-Equihua, Claudia A, Thrasher, Adrian J, Gaspar, H Bobby
Publicado 2009

Perforin Gene Transfer Into Hematopoietic Stem Cells Improves Immune Dysregulation in Murine Models of Perforin Deficiency

por Carmo, Marlene, Risma, Kimberly A, Arumugam, Paritha, Tiwari, Swati, Hontz, Adrianne E, Montiel-Equihua, Claudia A, Alonso-Ferrero, Maria E, Blundell, Michael P, Schambach, Axel, Baum, Christopher, Malik, Punam, Thrasher, Adrian J, Jordan, Michael B, Gaspar, H Bobby
Publicado 2015