Efficient engraftment and viral transduction of human hepatocytes in an FRG rat liver humanization model

por Carbonaro, Marisa, Lee, Jeffrey, Pefanis, Evangelos, Desclaux, Mathieu, Wang, Kehui, Pennington, Alexander, Huang, Hui, Mujica, Alejo, Rojas, Jose, Ally, Roxanne, Kennedy, Daniel, Brown, Michael, Rogulin, Vitaliy, Moller-Tank, Sven, Sabin, Leah, Zambrowicz, Brian, Thurston, Gavin, Li, Zhe
Publicado 2022

Production of large, defined genome modifications in rats by targeting rat embryonic stem cells

por Lee, Jeffrey, Wang, Jingjing, Ally, Roxanne, Trzaska, Sean, Hickey, Joseph, Mujica, Alejo, Miloscio, Lawrence, Mastaitis, Jason, Morse, Brian, Smith, Janell, Atanasio, Amanda, Chiao, Eric, Chen, Henry, Latuszek, Adrianna, Hu, Ying, Valenzuela, David, Romano, Carmelo, Zambrowicz, Brian, Auerbach, Wojtek
Publicado 2022

Cell type-selective targeted delivery of a recombinant lysosomal enzyme for enzyme therapies

por Baik, Andrew D., Calafati, Philip, Zhang, Xiaoli, Aaron, Nina A., Mehra, Antonia, Moller-Tank, Sven, Miloscio, Lawrence, Praggastis, Maria, Giovannone, Nicholas, Pan, Cheryl, Tang, Yajun, Bridges, Susannah, Mujica, Alejo, Barbounis, Peter, Yanolatos, Jean, Gale, Nicholas, Li, Ning, Kyratsous, Christos A., Schoenherr, Christopher J., Murphy, Andrew J., Economides, Aris N., Cygnar, Katherine D.
Publicado 2021