REAL‐world clinical effectiveness of ivacaftor therapy in the first 24 months in two infants with cystic fibrosis and different gating mutations—A case report

por Fuchs, Teresa, Appelt, Dorothea, Niedermayr, Katharina, Ellemunter, Helmut
Publicado 2022

Personalized medicine with drugs targeting the underlying protein defect in cystic fibrosis: is monitoring of treatment response necessary?

por Niedermayr, Katharina, Gasser, Verena, Rueckes-Nilges, Claudia, Appelt, Dorothea, Eder, Johannes, Fuchs, Teresa, Naehrlich, Lutz, Ellemunter, Helmut
Publicado 2022