Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Crigler-Najjar Syndrome

por Greig, Jenny A., Nordin, Jayme M.L., Draper, Christine, McMenamin, Deirdre, Chroscinski, Edward A., Bell, Peter, Gray, John T., Richman, Laura K., Wilson, James M.
Publicado 2018

Determining the Minimally Effective Dose of a Clinical Candidate Adeno-Associated Virus Vector in a Mouse Model of Hemophilia A

por Greig, Jenny A., Smith, Melanie K., Nordin, Jayme M.L., Goode, Tamara, Chroscinski, Edward A., Buza, Elizabeth L., Schmidt, Nicole, Kattenhorn, Lisa M., Wadsworth, Samuel, Wilson, James M.
Publicado 2022

AAV8 Gene Therapy for Crigler-Najjar Syndrome in Macaques Elicited Transgene T Cell Responses That Are Resident to the Liver

por Greig, Jenny A., Calcedo, Roberto, Kuri-Cervantes, Leticia, Nordin, Jayme M.L., Albrecht, Jessica, Bote, Erin, Goode, Tamara, Chroscinski, Edward A., Bell, Peter, Richman, Laura K., Betts, Michael R., Wilson, James M.
Publicado 2018

Profound phenotypic and epigenetic heterogeneity of the HIV-1-infected CD4(+) T cell reservoir

por Wu, Vincent H., Nordin, Jayme M. L., Nguyen, Son, Joy, Jaimy, Mampe, Felicity, del Rio Estrada, Perla M., Torres-Ruiz, Fernanda, González-Navarro, Mauricio, Luna-Villalobos, Yara Andrea, Ávila-Ríos, Santiago, Reyes-Terán, Gustavo, Tebas, Pablo, Montaner, Luis J., Bar, Katharine J., Vella, Laura A., Betts, Michael R.
Publicado 2022

Hepatic expression of GAA results in enhanced enzyme bioavailability in mice and non-human primates

por Costa-Verdera, Helena, Collaud, Fanny, Riling, Christopher R., Sellier, Pauline, Nordin, Jayme M. L., Preston, G. Michael, Cagin, Umut, Fabregue, Julien, Barral, Simon, Moya-Nilges, Maryse, Krijnse-Locker, Jacomina, van Wittenberghe, Laetitia, Daniele, Natalie, Gjata, Bernard, Cosette, Jeremie, Abad, Catalina, Simon-Sola, Marcelo, Charles, Severine, Li, Mathew, Crosariol, Marco, Antrilli, Tom, Quinn, William J., Gross, David A., Boyer, Olivier, Anguela, Xavier M., Armour, Sean M., Colella, Pasqualina, Ronzitti, Giuseppe, Mingozzi, Federico
Publicado 2021