Improving Care and Empowering Adults Living with SMA: A Call to Action in the New Treatment Era

por Walter, Maggie C., Chiriboga, Claudia, Duong, Tina, Goemans, Nathalie, Mayhew, Anna, Ouillade, Laëtitia, Oskoui, Maryam, Quinlivan, Ros, Vázquez-Costa, Juan F., Vissing, John, Servais, Laurent
Publicado 2021

Model consent clauses for rare disease research

por Nguyen, Minh Thu, Goldblatt, Jack, Isasi, Rosario, Jagut, Marlene, Jonker, Anneliene Hechtelt, Kaufmann, Petra, Ouillade, Laetitia, Molnar-Gabor, Fruszina, Shabani, Mahsa, Sid, Eric, Tassé, Anne Marie, Wong-Rieger, Durhane, Knoppers, Bartha Maria
Publicado 2019

Parents' dilemma: A therapeutic decision for children with spinal muscular atrophy (SMA) type 1

por Boursange, Sophie, Araneda, Marco, Stalens, Caroline, Desguerre, Isabelle, Barnerias, Christine, Nougues, Marie-Christine, Isapof, Arnaud, Quijano-Roy, Susana, Blu Genestine, Nadia, Ouillade, Laetitia, Martinez Jalilie, Maripaz, Castiglioni, Claudia, Boespflug-Tanguy, Odile, Gargiulo, Marcela
Publicado 2022