Micro-laminin gene therapy can function as an inhibitor of muscle disease in the dy(W) mouse model of MDC1A

por Packer, Davin, Martin, Paul T.
Publicado 2021

Remyelination in animal models of multiple sclerosis: finding the elusive grail of regeneration

por Packer, Davin, Fresenko, Emily E., Harrington, Em P.
Publicado 2023

Short-term treatment of golden retriever muscular dystrophy (GRMD) dogs with rAAVrh74.MHCK7.GALGT2 induces muscle glycosylation and utrophin expression but has no significant effec...

por Martin, Paul T., Zygmunt, Deborah A., Ashbrook, Anna, Hamilton, Sonia, Packer, Davin, Birch, Sharla M., Bettis, Amanda K., Balog-Alvarez, Cynthia J., Guo, Lee-Jae, Nghiem, Peter P., Kornegay, Joe N.
Publicado 2021

A first-in-human phase I/IIa gene transfer clinical trial for Duchenne muscular dystrophy using rAAVrh74.MCK.GALGT2

por Flanigan, Kevin M., Vetter, Tatyana A., Simmons, Tabatha R., Iammarino, Megan, Frair, Emma C., Rinaldi, Federica, Chicoine, Louis G., Harris, Johan, Cheatham, John P., Cheatham, Sharon L., Boe, Brian, Waldrop, Megan A., Zygmunt, Deborah A., Packer, Davin, Martin, Paul T.
Publicado 2022