Whole Body and CNS Biodistribution of rhHNS in Cynomolgus Monkeys after Intrathecal Lumbar Administration: Treatment Implications for Patients with MPS IIIA

por Chung, Jou-Ku, Pan, Luying, Palmieri, Kathleen, Youssef, Amir S., McCauley, Thomas G.
Publicado 2017

Biodistribution of Idursulfase Formulated for Intrathecal Use (Idursulfase-IT) in Cynomolgus Monkeys after Intrathecal Lumbar Administration

por Chung, Jou-Ku, Brown, Eilish, Crooker, Bob, Palmieri, Kathleen J., McCauley, Thomas G.
Publicado 2016

Myostatin and activin blockade by engineered follistatin results in hypertrophy and improves dystrophic pathology in mdx mouse more than myostatin blockade alone

por Iskenderian, Andrea, Liu, Nan, Deng, Qingwei, Huang, Yan, Shen, Chuan, Palmieri, Kathleen, Crooker, Robert, Lundberg, Dianna, Kastrapeli, Niksa, Pescatore, Brian, Romashko, Alla, Dumas, John, Comeau, Robert, Norton, Angela, Pan, Jing, Rong, Haojing, Derakhchan, Katayoun, Ehmann, David E.
Publicado 2018

Gene therapy for cross-correction of somatic organs and the CNS in mucopolysaccharidosis II in rodents and non-human primates

por Chen, Nancy, Ehmann, David E., Crooker, Robert, Derakhchan, Katayoun, Fang, Xiaodong, Felice, Brian, Galbreath, Elizabeth J., Glaus, Charles, Gu, Hongbo, Huang, Yan, Li, Christine, Li, Xing, Liu, Nan, Palmieri, Kathleen, Simic, Damir, Sypek, Joseph, Thompson, Susan, Winkelmann, Christopher T., Choi, Vivian W.
Publicado 2023