Subretinal timrepigene emparvovec in adult men with choroideremia: a randomized phase 3 trial

por MacLaren, Robert E., Fischer, M. Dominik, Gow, James A., Lam, Byron L., Sankila, Eeva-Marja K., Girach, Aniz, Panda, Sushil, Yoon, Dan, Zhao, Guolin, Pennesi, Mark E.
Publicado 2023