CRISPR Activation Enhances In Vitro Potency of AAV Vectors Driven by Tissue-Specific Promoters

por McDougald, Devin S., Duong, Thu T., Palozola, Katherine C., Marsh, Anson, Papp, Tyler E., Mills, Jason A., Zhou, Shangzhen, Bennett, Jean
Publicado 2019

Identification of a novel pathogenic missense mutation in PRPF31 using whole exome sequencing: a case report

por Bryant, Laura, Lozynska, Olga, Marsh, Anson, Papp, Tyler E, van Gorder, Lucas, Serrano, Leona W, Gai, Xiaowu, Maguire, Albert M, Aleman, Tomas S, Bennett, Jean
Publicado 2019

Highly efficient CD4+ T cell targeting and genetic recombination using engineered CD4+ cell-homing mRNA-LNPs

por Tombácz, István, Laczkó, Dorottya, Shahnawaz, Hamna, Muramatsu, Hiromi, Natesan, Ambika, Yadegari, Amir, Papp, Tyler E., Alameh, Mohamad-Gabriel, Shuvaev, Vladimir, Mui, Barbara L., Tam, Ying K., Muzykantov, Vladimir, Pardi, Norbert, Weissman, Drew, Parhiz, Hamideh
Publicado 2021

Added to pre-existing inflammation, mRNA-lipid nanoparticles induce inflammation exacerbation (IE)

por Parhiz, Hamideh, Brenner, Jacob S., Patel, Priyal N., Papp, Tyler E., Shahnawaz, Hamna, Li, Qin, Shi, Ruiqi, Zamora, Marco E., Yadegari, Amir, Marcos-Contreras, Oscar A., Natesan, Ambika, Pardi, Norbert, Shuvaev, Vladimir V., Kiseleva, Raisa, Myerson, Jacob W., Uhler, Thomas, Riley, Rachel S., Han, Xuexiang, Mitchell, Michael J., Lam, Kieu, Heyes, James, Weissman, Drew, Muzykantov, Vladimir R.
Publicado 2022