Enabling endpoint development for interventional clinical trials in individuals with Angelman syndrome: a prospective, longitudinal, observational clinical study (FREESIAS)

por Tjeertes, Jorrit, Bacino, Carlos A., Bichell, Terry Jo, Bird, Lynne M., Bustamante, Mariana, Crean, Rebecca, Jeste, Shafali, Komorowski, Robert W., Krishnan, Michelle L., Miller, Meghan T., Nobbs, David, Ochoa-Lubinoff, Cesar, Parkerson, Kimberly A., Rotenberg, Alexander, Sadhwani, Anjali, Shen, Mark D., Squassante, Lisa, Tan, Wen-Hann, Vincenzi, Brenda, Wheeler, Anne C., Hipp, Joerg F., Berry-Kravis, Elizabeth
Publicado 2023