Muscle‐directed gene therapy corrects Pompe disease and uncovers species‐specific GAA immunogenicity

por Eggers, Michelle, Vannoy, Charles H, Huang, Jianyong, Purushothaman, Pravinkumar, Brassard, Jacqueline, Fonck, Carlos, Meng, Hui, Prom, Mariah J, Lawlor, Michael W, Cunningham, Justine, Sadhu, Chanchal, Mavilio, Fulvio
Publicado 2021

Voluntary wheel running complements microdystrophin gene therapy to improve muscle function in mdx mice

por Hamm, Shelby E., Fathalikhani, Daniel D., Bukovec, Katherine E., Addington, Adele K., Zhang, Haiyan, Perry, Justin B., McMillan, Ryan P., Lawlor, Michael W., Prom, Mariah J., Vanden Avond, Mark A., Kumar, Suresh N., Coleman, Kirsten E., Dupont, J.B., Mack, David L., Brown, David A., Morris, Carl A., Gonzalez, J. Patrick, Grange, Robert W.
Publicado 2021

Voluntary wheel running complements microdystrophin gene therapy to improve muscle function in mdx mice

por Hamm, Shelby E., Fathalikhani, Daniel D., Bukovec, Katherine E., Addington, Adele K., Zhang, Haiyan, Perry, Justin B., McMillan, Ryan P., Lawlor, Michael W., Prom, Mariah J., Vanden Avond, Mark A., Kumar, Suresh N., Coleman, Kirsten E., Dupont, J.B., Mack, David L., Brown, David A., Morris, Carl A., Gonzalez, J. Patrick, Grange, Robert W.
Publicado 2021