Genome editing for blood disorders: state of the art and recent advances

por Romito, Marianna, Rai, Rajeev, Thrasher, Adrian J., Cavazza, Alessia
Publicado 2019

Designer epigenome modifiers enable robust and sustained gene silencing in clinically relevant human cells

por Mlambo, Tafadzwa, Nitsch, Sandra, Hildenbeutel, Markus, Romito, Marianna, Müller, Maximilian, Bossen, Claudia, Diederichs, Sven, Cornu, Tatjana I, Cathomen, Toni, Mussolino, Claudio
Publicado 2018

Targeted gene correction of human hematopoietic stem cells for the treatment of Wiskott - Aldrich Syndrome

por Rai, Rajeev, Romito, Marianna, Rivers, Elizabeth, Turchiano, Giandomenico, Blattner, Georges, Vetharoy, Winston, Ladon, Dariusz, Andrieux, Geoffroy, Zhang, Fang, Zinicola, Marta, Leon-Rico, Diego, Santilli, Giorgia, Thrasher, Adrian J., Cavazza, Alessia
Publicado 2020