CRISPR-Cas9 generated Pompe knock-in murine model exhibits early-onset hypertrophic cardiomyopathy and skeletal muscle weakness

por Huang, Jeffrey Y., Kan, Shih-Hsin, Sandfeld, Emilie K., Dalton, Nancy D., Rangel, Anthony D., Chan, Yunghang, Davis-Turak, Jeremy, Neumann, Jon, Wang, Raymond Y.
Publicado 2020