Adeno Associated Viral Vector Delivered RNAi for Gene Therapy of SOD1 Amyotrophic Lateral Sclerosis

por Stoica, Lorelei, Sena-Esteves, Miguel
Publicado 2016

DIPG-17. TREATMENT OF DIFFUSE INTRINSIC PONTINE GLIOMA USING ALLELE-SPECIFIC SIRNA TARGETING H3.3 K27M MUTANT HISTONE

por Wentworth, Simon, Batista, Ana Rita, Alterman, Julia, Khvorova, Anastasia, Sena-Esteves, Miguel
Publicado 2023

Intracranial AAV‐IFN‐β gene therapy eliminates invasive xenograft glioblastoma and improves survival in orthotopic syngeneic murine model

por GuhaSarkar, Dwijit, Neiswender, James, Su, Qin, Gao, Guangping, Sena‐Esteves, Miguel
Publicado 2017

Pig’s ear: Streptococcus suis Meningitis and its associated inner ear implications

por Sena Esteves, S., Carvalho de Almeida, J., Abrunhosa, J., Almeida e Sousa, C., Arshad, Q.
Publicado 2017

Evaluation of aesthetic and functional outcomes in rhinoplasty surgery: a prospective study()

por Sena Esteves, Sara, Gonçalves Ferreira, Miguel, Carvalho Almeida, João, Abrunhosa, José, Almeida e Sousa, Cecília
Publicado 2016

Targeting HSV-1 virions for specific binding to epidermal growth factor receptor-vIII bearing tumor cells

por Grandi, Paola, Fernandez, Juliet, Szentirmai, Oscar, Carter, Robert, Gianni, Davide, Sena-Esteves, Miguel, Breakefield, Xandra O.
Publicado 2010

Frameless multimodal image guidance of localized convection-enhanced delivery of therapeutics in the brain

por van der Bom, Imramsjah M J, Moser, Richard P, Gao, Guanping, Sena-Esteves, Miguel, Aronin, Neil, Gounis, Matthew J
Publicado 2013

OR18-1 The Impact of Makorin Ring Finger Protein 3 (MKRN3) Overexpression in the Arcuate Nucleus of Postpubertal Female Mice on the HPG Axis

por Carroll, Rona, Kaiser, Ursula, Kim, Han Kyeol, McKnight, Kali, Naule, Lydie, Pereira, Sidney, Sena-Esteves, Miguel, Roberts, Stephanie
Publicado 2022

Imaging gene delivery in a mouse model of congenital neuronal ceroid lipofuscinosis

por Pike, Lisa S., Tannous, Bakhos A., Deliolanis, Nikolaos C., Hsich, Gary, Morse, Danielle, Tung, Ching-Hsuan, Sena-Esteves, Miguel, Breakefield, Xandra O.
Publicado 2011

Glioblastoma microvesicles transport RNA and protein that promote tumor growth and provide diagnostic biomarkers

por Skog, Johan, Wurdinger, Tom, van Rijn, Sjoerd, Meijer, Dimphna, Gainche, Laura, Sena-Esteves, Miguel, Curry, William T., Carter, Robert S., Krichevsky, Anna M., Breakefield, Xandra O.
Publicado 2008

Autophagy Activation by Transcription Factor EB (TFEB) in Striatum of HD(Q175/Q7) Mice

por Vodicka, Petr, Chase, Kathryn, Iuliano, Maria, Tousley, Adelaide, Valentine, Dana T., Sapp, Ellen, Kegel-Gleason, Kimberly B., Sena-Esteves, Miguel, Aronin, Neil, DiFiglia, Marian
Publicado 2016

Human GLB1 knockout cerebral organoids: A model system for testing AAV9-mediated GLB1 gene therapy for reducing GM1 ganglioside storage in GM1 gangliosidosis

por Latour, Yvonne L., Yoon, Robin, Thomas, Sarah E., Grant, Christina, Li, Cuiling, Sena-Esteves, Miguel, Allende, Maria L., Proia, Richard L., Tifft, Cynthia J.
Publicado 2019

AAV-Mediated Gene Delivery in Adult GM1-Gangliosidosis Mice Corrects Lysosomal Storage in CNS and Improves Survival

por Baek, Rena C., Broekman, Marike L. D., Leroy, Stanley G., Tierney, Laryssa A., Sandberg, Michael A., d'Azzo, Alessandra, Seyfried, Thomas N., Sena-Esteves, Miguel
Publicado 2010

Triple Bioluminescence Imaging for In Vivo Monitoring of Cellular Processes

por Maguire, Casey A, Bovenberg, M Sarah, Crommentuijn, Matheus HW, Niers, Johanna M, Kerami, Mariam, Teng, Jian, Sena-Esteves, Miguel, Badr, Christian E, Tannous, Bakhos A
Publicado 2013

Cerebral organoids derived from Sandhoff disease-induced pluripotent stem cells exhibit impaired neurodifferentiation

por Allende, Maria L., Cook, Emily K., Larman, Bridget C., Nugent, Adrienne, Brady, Jacqueline M., Golebiowski, Diane, Sena-Esteves, Miguel, Tifft, Cynthia J., Proia, Richard L.
Publicado 2018

Stochastic Model of Tsc1 Lesions in Mouse Brain

por Prabhakar, Shilpa, Goto, June, Zuang, Xuan, Sena-Esteves, Miguel, Bronson, Roderick, Brockmann, Jillian, Gianni, Davide, Wojtkiewicz, Gregory R., Chen, John W., Stemmer-Rachamimov, Anat, Kwiatkowski, David J., Breakefield, Xandra O.
Publicado 2013

Correction: Stochastic Model of Tsc1 Lesions in Mouse Brain

por Prabhakar, Shilpa, Goto, June, Zhang, Xuan, Sena-Esteves, Miguel, Bronson, Roderick, Brockmann, Jillian, Gianni, Davide, Wojtkiewicz, Gregory R., Chen, John W., Stemmer-Rachamimov, Anat, Kwiatkowski, David J., Breakefield, Xandra O.
Publicado 2013

Lipidomic Evaluation of Feline Neurologic Disease after AAV Gene Therapy

por Gray-Edwards, Heather L., Jiang, Xuntian, Randle, Ashley N., Taylor, Amanda R., Voss, Taylor L., Johnson, Aime K., McCurdy, Victoria J., Sena-Esteves, Miguel, Ory, Daniel S., Martin, Douglas R.
Publicado 2017

Upregulating β-hexosaminidase activity in rodents prevents α-synuclein lipid associations and protects dopaminergic neurons from α-synuclein-mediated neurotoxicity

por Brekk, Oeystein R., Korecka, Joanna A., Crapart, Cecile C., Huebecker, Mylene, MacBain, Zachary K., Rosenthal, Sara Ann, Sena-Esteves, Miguel, Priestman, David A., Platt, Frances M., Isacson, Ole, Hallett, Penelope J.
Publicado 2020

Adeno-Associated Virus Neutralizing Antibodies in Large Animals and Their Impact on Brain Intraparenchymal Gene Transfer

por Wang, Dan, Zhong, Li, Li, Mengxin, Li, Jia, Tran, Karen, Ren, Lingzhi, He, Ran, Xie, Jun, Moser, Richard P., Fraser, Cara, Kuchel, Tim, Sena-Esteves, Miguel, Flotte, Terence R., Aronin, Neil, Gao, Guangping
Publicado 2018