Various AAV Serotypes and Their Applications in Gene Therapy: An Overview

por Issa, Shaza S., Shaimardanova, Alisa A., Solovyeva, Valeriya V., Rizvanov, Albert A.
Publicado 2023

Gene Therapy of Sphingolipid Metabolic Disorders

por Shaimardanova, Alisa A., Solovyeva, Valeriya V., Issa, Shaza S., Rizvanov, Albert A.
Publicado 2023

Functionality of a bicistronic construction containing HEXA and HEXB genes encoding β-hexosaminidase A for cell-mediated therapy of GM2 gangliosidoses

por Shaimardanova, Alisa A., Chulpanova, Daria S., Solovyeva, Valeriya V., Aimaletdinov, Aleksandr M., Rizvanov, Albert A.
Publicado 2021

Mesenchymal Stem Cell-Based Therapy for Lysosomal Storage Diseases and Other Neurodegenerative Disorders

por Issa, Shaza S., Shaimardanova, Alisa A., Valiullin, Victor V., Rizvanov, Albert A., Solovyeva, Valeriya V.
Publicado 2022

Current Strategies for the Gene Therapy of Autosomal Recessive Congenital Ichthyosis and Other Types of Inherited Ichthyosis

por Chulpanova, Daria S., Shaimardanova, Alisa A., Ponomarev, Aleksei S., Elsheikh, Somaia, Rizvanov, Albert A., Solovyeva, Valeriya V.
Publicado 2022

Safety and Efficacy of Intravenous and Intrathecal Delivery of AAV9-Mediated ARSA in Minipigs

por Mullagulova, Aysilu, Shaimardanova, Alisa, Solovyeva, Valeriya, Mukhamedshina, Yana, Chulpanova, Daria, Kostennikov, Alexander, Issa, Shaza, Rizvanov, Albert
Publicado 2023

New Approaches to Tay-Sachs Disease Therapy

por Solovyeva, Valeriya V., Shaimardanova, Alisa A., Chulpanova, Daria S., Kitaeva, Kristina V., Chakrabarti, Lisa, Rizvanov, Albert A.
Publicado 2018

Extracellular vesicles in the diagnosis and treatment of central nervous system diseases

por Shaimardanova, Alisa A., Solovyeva, Valeriya V., Chulpanova, Daria S., James, Victoria, Kitaeva, Kristina V., Rizvanov, Albert A.
Publicado 2019

Metachromatic Leukodystrophy: Diagnosis, Modeling, and Treatment Approaches

por Shaimardanova, Alisa A., Chulpanova, Daria S., Solovyeva, Valeriya V., Mullagulova, Aysilu I., Kitaeva, Kristina V., Allegrucci, Cinzia, Rizvanov, Albert A.
Publicado 2020

Gene and Cell Therapy for Epilepsy: A Mini Review

por Shaimardanova, Alisa A., Chulpanova, Daria S., Mullagulova, Aysilu I., Afawi, Zaid, Gamirova, Rimma G., Solovyeva, Valeriya V., Rizvanov, Albert A.
Publicado 2022

Production and Application of Multicistronic Constructs for Various Human Disease Therapies

por Shaimardanova, Alisa A., Chulpanova, Daria S., Kitaeva, Kristina V., Abdrakhmanova, Ilmira I., Chernov, Vladislav M., Rutland, Catrin S., Rizvanov, Albert A., Solovyeva, Valeriya V.
Publicado 2019

Increasing β-hexosaminidase A activity using genetically modified mesenchymal stem cells

por Shaimardanova, Alisa A., Chulpanova, Daria S., Solovyeva, Valeriya V., Issa, Shaza S., Mullagulova, Aysilu I., Titova, Angelina A., Mukhamedshina, Yana O., Timofeeva, Anna V., Aimaletdinov, Alexander M., Nigmetzyanov, Islam R., Rizvanov, Albert A.
Publicado 2023

Serum Cytokine Profile, Beta-Hexosaminidase A Enzymatic Activity and GM(2) Ganglioside Levels in the Plasma of a Tay-Sachs Disease Patient after Cord Blood Cell Transplantation and...

por Shaimardanova, Alisa A., Chulpanova, Daria S., Solovyeva, Valeriya V., Garanina, Ekaterina E., Salafutdinov, Ilnur I., Laikov, Alexander Vladimirovich, Kursenko, Vadim V., Chakrabarti, Lisa, Zakharova, Ekaterina Yu., Bukina, Tatiana M., Baydakova, Galina V., Rizvanov, Albert Anatolyevich
Publicado 2021