OR21-3 Familial Chylomicronemia Syndrome: Distinguishing the Rare Among the Common in Adults for Appropriate Management

por Ueda, Masako, Burke, Frances, Sviridov, Denis, Escobar, Maria, Walters, Laura, Lalic, Dusanka, Sikora, Tracey, Greene, Harley, DerOhannessian, Stephanie, McIntyre, Adam, deGoma, Emil, Remaley, Alan, Hegele, Robert, Rader, Daniel, Dunbar, Richard
Publicado 2019

Evaluation of AAV-mediated Gene Therapy for Central Nervous System Disease in Canine Mucopolysaccharidosis VII

por Gurda, Brittney L, De Guilhem De Lataillade, Adrien, Bell, Peter, Zhu, Yanqing, Yu, Hongwei, Wang, Ping, Bagel, Jessica, Vite, Charles H, Sikora, Tracey, Hinderer, Christian, Calcedo, Roberto, Yox, Alexander D, Steet, Richard A, Ruane, Therese, O'Donnell, Patricia, Gao, Guangping, Wilson, James M, Casal, Margret, Ponder, Katherine P, Haskins, Mark E
Publicado 2016