Seeing through Musculoskeletal Tissues: Improving In Situ Imaging of Bone and the Lacunar Canalicular System through Optical Clearing

por Berke, Ian M., Miola, Joseph P., David, Michael A., Smith, Melanie K., Price, Christopher
Publicado 2016

Lipid nanoparticle-encapsulated mRNA therapy corrects serum total bilirubin level in Crigler-Najjar syndrome mouse model

por Greig, Jenny A., Chorazeczewski, Joanna K., Chowdhary, Vivek, Smith, Melanie K., Jennis, Matthew, Tarrant, James C., Buza, Elizabeth L., Coughlan, Kimberly, Martini, Paolo G.V., Wilson, James M.
Publicado 2023

Determining the Minimally Effective Dose of a Clinical Candidate Adeno-Associated Virus Vector in a Mouse Model of Hemophilia A

por Greig, Jenny A., Smith, Melanie K., Nordin, Jayme M.L., Goode, Tamara, Chroscinski, Edward A., Buza, Elizabeth L., Schmidt, Nicole, Kattenhorn, Lisa M., Wadsworth, Samuel, Wilson, James M.
Publicado 2022

Treating Transthyretin Amyloidosis via Adeno-Associated Virus Vector Delivery of Meganucleases

por Greig, Jenny A., Breton, Camilo, Ashley, Scott N., Martins, Kelly M., Gorsuch, Cassandra, Chorazeczewski, Joanna K., Furmanak, Thomas, Smith, Melanie K., Zhu, Yanqing, Bell, Peter, Shoop, Wendy, Li, Hui, Smith, Jeff, Tomberlin, Ginger, Clark, Peter, Mitchell, Thomas W., Buza, Elizabeth L., Yan, Hanying, Jantz, Derek, Wilson, James M.
Publicado 2022