Very Low Residual Dystrophin Quantity Is Associated with Milder Dystrophinopathy

por de Feraudy, Yvan, Ben Yaou, Rabah, Wahbi, Karim, Stalens, Caroline, Stantzou, Amalia, Laugel, Vincent, Desguerre, Isabelle, Servais, Laurent, Leturcq, France, Amthor, Helge
Publicado 2020

Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle

por Morin, Adrien, Stantzou, Amalia, Petrova, Olga N., Hildyard, John, Tensorer, Thomas, Matouk, Meriem, Petkova, Mina V., Richard, Isabelle, Manoliu, Tudor, Goyenvalle, Aurélie, Falcone, Sestina, Schuelke, Markus, Laplace-Builhé, Corinne, Piercy, Richard J., Garcia, Luis, Amthor, Helge
Publicado 2023