Commentary on the 2023 ASH guidelines for thrombophilia testing in venous thromboembolism

por Juneja, Manu, Szer, Jeff
Publicado 2023

Normalisation of haemoglobin and control of breakthrough haemolysis with increased frequency pegcetacoplan dosing in treated paroxysmal nocturnal haemoglobinuria

por Davis, Amanda K., Bingham, Nicholas, Szer, Jeff
Publicado 2023

The impact of COVID-19 on the provision of donor hematopoietic stem cell products worldwide: collateral damage

por Szer, Jeff, Weisdorf, Daniel, Querol, Sergio, Foeken, Lydia, Madrigal, Alejandro
Publicado 2020

High-Dose Ambroxol Therapy in Type 1 Gaucher Disease Focusing on Patients with Poor Response to Enzyme Replacement Therapy or Substrate Reduction Therapy

por Istaiti, Majdolen, Frydman, Dafna, Dinur, Tama, Szer, Jeff, Revel-Vilk, Shoshana, Zimran, Ari
Publicado 2023

The Bone Biomarker of Quantitative Chemical Shift Imaging in Patients with Type 1 Gaucher Disease Receiving Low-Dose Long-Term Enzyme Replacement Therapy

por Zimran, Ari, Szer, Jeff, Becker-Cohen, Michal, Jens, Sjoerd, Cozma, Claudia, Revel-Vilk, Shoshana
Publicado 2023

Patient reported outcome measures in a large cohort of patients with type 1 Gaucher disease

por Dinur, Tama, Istaiti, Majdolen, Frydman, Dafna, Becker-Cohen, Michal, Szer, Jeff, Zimran, Ari, Revel-Vilk, Shoshana
Publicado 2020

PB2064: THE COMPLETE STUDY: A SINGLE ARM, MULTICENTER OBSERVATIONAL STUDY TO EVALUATE EFFECTIVENESS OF PEGCETACOPLAN UNDER REAL WORLD CONDITIONS IN PATIENTS WITH PAROXYSMAL NOCTURN...

por de Latour, Régis Peffault, Szer, Jeff, Kulasekararaj, Austin, Gaya, Anna, Sica, Simona, Nölte, Matthias, Horneff, Regina, Stefan, Lethagen
Publicado 2023

Effects of intensive induction and consolidation chemotherapy with idarubicin and high dose cytarabine on minimal residual disease levels in newly diagnosed adult precursor-B acute...

por Bradstock, Kenneth F., Morley, Alec, Byth, Karen, Szer, Jeff, Prosser, Ian, Cannell, Paul, Irving, Ian, Seymour, John F.
Publicado 2016

Infective hyperammonaemic encephalopathy after allogeneic stem cell transplant

por Shipton, Michael J., Kinsella, Paul M., Davis, Thomas, Azzato, Francesca, Taiaroa, George, Szer, Jeff, Routledge, David, Smibert, Olivia
Publicado 2022

Prognostic value of blood biomarkers in steroid-refractory or steroid-dependent acute graft-versus-host disease: a REACH2 analysis

por Socié, Gerard, Niederwieser, Dietger, von Bubnoff, Nikolas, Mohty, Mohamad, Szer, Jeff, Or, Reuven, Garrett, James, Prahallad, Anirudh, Wilke, Celine, Zeiser, Robert
Publicado 2023

Composite endpoint to evaluate complement inhibition therapy in patients with paroxysmal nocturnal hemoglobinuria

por Kulasekararaj, Austin, Glasmacher, Axel, Liu, Peng, Szer, Jeff, Araten, David, Rauch, Geraldine, Gwaltney, Chad, Sierra, J Rafael, Lee, Jong Wook
Publicado 2022

P781: EVALUATION OF PEGCETACOPLAN TREATMENT SUCCESS IN PAROXYSMAL NOCTURNAL HEMOGLOBINURIA WITH AND WITHOUT BONE MARROW FAILURE: A MOVE TOWARDS INDIVIDUALIZED PATIENT TREATMENT

por Szer, Jeff, Panse, Jens, Kulasekararaj, Austin, Oliver, Monika, Fattizzo, Bruno, Nishimura, Jun-Ichi, Szamosi, Johan, Horneff, Regina, Peffault de Latour, Régis
Publicado 2023

Phase 3 Study of Subcutaneous Versus Intravenous Ravulizumab in Eculizumab-Experienced Adult Patients with PNH: Primary Analysis and 1-Year Follow-Up

por Yenerel, Mustafa N., Sicre de Fontbrune, Flore, Piatek, Caroline, Sahin, Fahri, Füreder, Wolfgang, Ortiz, Stephan, Ogawa, Masayo, Ozol-Godfrey, Ayca, Sierra, J. Rafael, Szer, Jeff
Publicado 2022

Real-World Experiences with Taliglucerase Alfa Home Infusions for Patients with Gaucher Disease: A Global Cohort Study

por Revel-Vilk, Shoshana, Mansfield, Royston, Feder-Krengel, Neta, Machtiger-Azoulay, Noya, Kuter, David, Szer, Jeff, Rosenbaum, Hanna, Ferreira, David Cavalcanti, Ruhrman-Shahar, Noa, Wajnrajch, Michael, Zimran, Ari
Publicado 2023

Immune thrombocytopenia following immunisation with Vaxzevria ChadOx1-S (AstraZeneca) vaccine, Victoria, Australia

por Gordon, Sally F., Clothier, Hazel J., Morgan, Hannah, Buttery, Jim P., Phuong, Linny K., Monagle, Paul, Chunilal, Sanjeev, Wood, Erica M., Tran, Huyen, Szer, Jeff, Crawford, Nigel W.
Publicado 2021

P772: LONG-TERM RAVULIZUMAB TREATMENT IN COMPLEMENT INHIBITOR-EXPERIENCED PATIENTS WITH PNH PROVIDES DURABLE CONTROL OF INTRAVASCULAR HEMOLYSIS WITH LOW INCIDENCE OF MAJOR ADVERSE...

por Kulasekararaj, Austin, Brodsky, Robert, Griffin, Morag, Röth, Alexander, Piatek, Caroline, Ogawa, Masayo, Yu, Ji, Patel, Yogesh, Fernandez, Fernando Ataulfo Gonzalez, Nishimura, Jun-Ichi, Peffault de Latour, Régis, Szer, Jeff, Wook Lee, Jong
Publicado 2023

Pharmacokinetic and pharmacodynamic effects of ravulizumab and eculizumab on complement component 5 in adults with paroxysmal nocturnal haemoglobinuria: results of two phase 3 rand...

por Peffault de Latour, Régis, Brodsky, Robert A., Ortiz, Stephan, Risitano, Antonio M., Jang, Jun H., Hillmen, Peter, Kulagin, Alexander D., Kulasekararaj, Austin G., Rottinghaus, Scott T., Aguzzi, Rasha, Gao, Xiang, Wells, Richard A., Szer, Jeff
Publicado 2020

Changes in Hematopoietic Cell Transplantation Practices in Response to COVID-19: A Survey from the Worldwide Network for Blood & Marrow Transplantation

por Worel, Nina, Shaw, Bronwen E., Aljurf, Mahmoud, Koh, Mickey, Seber, Adriana, Weisdorf, Daniel, Schwartz, Joseph, Galeano, Sebastian, Kodera, Yoshihisa, Eldridge, Paul W., Hashmi, Shahrukh, Atsuta, Yoshiko, Szer, Jeff, Saber, Wael, Niederwieser, Dietger, Greinix, Hildegard T.
Publicado 2021

Recommended screening and preventive practices for long-term survivors after hematopoietic cell transplantation

por Majhail, Navneet Singh, Rizzo, James Douglas, Lee, Stephanie Joi, Aljurf, Mahmoud, Atsuta, Yoshiko, Bonfim, Carmem, Burns, Linda Jean, Chaudhri, Naeem, Davies, Stella, Okamoto, Shinichiro, Seber, Adriana, Socie, Gerard, Szer, Jeff, Lint, Maria Teresa Van, Wingard, John Reid, Tichelli, Andre
Publicado 2012

Characterization of breakthrough hemolysis events observed in the phase III randomized studies of ravulizumab versus eculizumab in adults with paroxysmal nocturnal hemoglobinuria

por Brodsky, Robert A., de Latour, Régis Peffault, Rottinghaus, Scott T., Röth, Alexander, Risitano, Antonio M., Weitz, Ilene C., Hillmen, Peter, Maciejewski, Jaroslaw P., Szer, Jeff, Lee, Jong Wook, Kulasekararaj, Austin G., Volles, Lori, Damokosh, Andrew I., Ortiz, Stephan, Shafner, Lori, Liu, Peng, Hill, Anita, Schrezenmeier, Hubert
Publicado 2020