Reduction of lysosome abundance and GAG accumulation after odiparcil treatment in MPS I and MPS VI models

por Tuyaa-Boustugue, Pascale, Jantzen, Ingrid, Zhang, Haoyue, Young, Sarah P., Broqua, Pierre, Tallandier, Mireille, Entchev, Eugeni
Publicado 2023

Odiparcil, a potential glycosaminoglycans clearance therapy in mucopolysaccharidosis VI—Evidence from in vitro and in vivo models

por Entchev, Eugeni, Jantzen, Ingrid, Masson, Philippe, Bocart, Stephanie, Bournique, Bruno, Luccarini, Jean-Michel, Bouchot, Andre, Lacombe, Olivier, Junien, Jean-Louis, Broqua, Pierre, Tallandier, Mireille
Publicado 2020