A Race Against Time—Changing the Natural History of CRIM Negative Infantile Pompe Disease

por Gupta, Punita, Shayota, Brian J., Desai, Ankit K., Kiblawi, Fuad, Myridakis, Dorothy, Messina, John, Tah, Peter, Tambini-King, Lorien, Kishnani, Priya S.
Publicado 2020