Etranacogene dezaparvovec for hemophilia B gene therapy

por Thornburg, Courtney D.
Publicado 2021

Gene Therapy for Hemophilia A: A Mixed Methods Study of Patient Preferences and Shared Decision-Making

por Limjoco, Jacqueline, Thornburg, Courtney D
Publicado 2023

Venous Thromboembolism in Children with Cancer and Blood Disorders

por Ko, Richard H., Thornburg, Courtney D.
Publicado 2017

Treatment adherence in hemophilia

por Thornburg, Courtney D, Duncan, Natalie A
Publicado 2017

Evaluating Gene Therapy as a Potential Paradigm Shift in Treating Severe Hemophilia

por Thornburg, Courtney D., Simmons, Dana H., von Drygalski, Annette
Publicado 2023

Direct oral anticoagulants in pediatric venous thromboembolism: Experience in specialized pediatric hemostasis centers in the United States

por Corrales-Medina, Fernando F., Raffini, Leslie, Recht, Michael, Santos, Jarren, Thornburg, Courtney D., Davila, Jennifer
Publicado 2022

A 2-year-old girl with co-inherited cystic fibrosis and sickle cell-β(+) thalassemia presenting with recurrent vaso-occlusive events during cystic fibrosis pulmonary exacerbations:...

por Sobush, Kurtis T, Thornburg, Courtney D, Voynow, Judith A, Davis, Stephanie D, Peterson-Carmichael, Stacey L
Publicado 2013

Utilization of Telemedicine for Comprehensive Visits in Patients with Inherited Bleeding Disorders during the COVID-19 Pandemic

por Wang, Cassandra P, Bush, Kelly Ann, Brooks, Rosalie, Farrow, Katharine, Gilsdorf, Lizandra, Cortez, Fernanda, Thornburg, Courtney D
Publicado 2020

Assessment of Factors Associated With Parental Perceptions of Voluntary Decisions About Child Participation in Leukemia Clinical Trials

por Aristizabal, Paula, Ma, Arissa K., Kumar, Nikhil V., Perdomo, Bianca P., Thornburg, Courtney D., Martinez, Maria Elena, Nodora, Jesse
Publicado 2021

Health care resource utilization and costs among adult patients with hemophilia A on factor VIII prophylaxis: an administrative claims analysis

por Croteau, Stacy E, Cook, Keziah, Sheikh, Lamiya, Chawla, Anita, Sammon, Joshua, Solari, Paul, Kim, Benjamin, Hinds, David, Thornburg, Courtney D
Publicado 2021

Recombinant Activated Factor VIIa Treatment for Refractory Hemorrhage in Infants

por Dang, Chi N, Katakam, Lakshmi I, Smith, P Brian, Cotten, C Michael, Goldberg, Ronald N, Chandler, Nicole, Thornburg, Courtney D, Bidegain, Margarita
Publicado 2010

The odds and implications of coinheritance of hemophilia A and B

por Karch, Corinne, Masser‐Frye, Diane, Limjoco, Jacqueline, Ryan, Sarah E., Fletcher, Shelley N., Corbett, Kevin D., Johnsen, Jill M., Thornburg, Courtney D.
Publicado 2020

Extracellular tyrosyl‐tRNA synthetase cleaved by plasma proteinases and stored in platelet α‐granules: Potential role in monocyte activation

por Won, Eric, Morodomi, Yosuke, Kanaji, Sachiko, Shapiro, Ryan, Vo, My‐Nuong, Orje, Jennifer N., Thornburg, Courtney D., Yang, Xiang‐Lei, Ruggeri, Zaverio M., Schimmel, Paul, Kanaji, Taisuke
Publicado 2020

Identification and characterization of novel mutations implicated in congenital fibrinogen disorders

por Smith, Natalie, Bornikova, Larissa, Noetzli, Leila, Guglielmone, Hugo, Minoldo, Salvador, Backos, Donald S., Jacobson, Linda, Thornburg, Courtney D., Escobar, Miguel, White‐Adams, Tara C., Wolberg, Alisa S., Manco‐Johnson, Marilyn, Di Paola, Jorge
Publicado 2018

Improving Pediatric Neuro-Oncology Survival Disparities in the United States–Mexico Border Region: A Cross-Border Initiative Between San Diego, California, and Tijuana, Mexico

por Aristizabal, Paula, Burns, Luke P., Kumar, Nikhil V., Perdomo, Bianca P., Rivera-Gomez, Rebeca, Ornelas, Mario A., Gonda, David, Malicki, Denise, Thornburg, Courtney D., Roberts, William, Levy, Michael L., Crawford, John R.
Publicado 2020

Cost Efficacy of Rapid Whole Genome Sequencing in the Pediatric Intensive Care Unit

por Sanford Kobayashi, Erica, Waldman, Bryce, Engorn, Branden M., Perofsky, Katherine, Allred, Erika, Briggs, Benjamin, Gatcliffe, Chelsea, Ramchandar, Nanda, Gold, Jeffrey J., Doshi, Ami, Ingulli, Elizabeth G., Thornburg, Courtney D., Benson, Wendy, Farnaes, Lauge, Chowdhury, Shimul, Rego, Seema, Hobbs, Charlotte, Kingsmore, Stephen F., Dimmock, David P., Coufal, Nicole G.
Publicado 2022