Failures to further developing orphan medicinal products after designation granted in Europe: an analysis of marketing authorisation failures and abandoned drugs

por Giannuzzi, Viviana, Landi, Annalisa, Bosone, Enrico, Giannuzzi, Floriana, Nicotri, Stefano, Torrent-Farnell, Josep, Bonifazi, Fedele, Felisi, Mariagrazia, Bonifazi, Donato, Ceci, Adriana
Publicado 2017

Evidence supporting regulatory-decision making on orphan medicinal products authorisation in Europe: methodological uncertainties

por Pontes, Caridad, Fontanet, Juan Manuel, Vives, Roser, Sancho, Aranzazu, Gómez-Valent, Mònica, Ríos, José, Morros, Rosa, Martinalbo, Jorge, Posch, Martin, Koch, Armin, Roes, Kit, Rengerink, Katrien Oude, Torrent-Farnell, Josep, Torres, Ferran
Publicado 2018

Recommendations from the European Working Group for Value Assessment and Funding Processes in Rare Diseases (ORPH-VAL)

por Annemans, Lieven, Aymé, Ségolène, Le Cam, Yann, Facey, Karen, Gunther, Penilla, Nicod, Elena, Reni, Michele, Roux, Jean-Louis, Schlander, Michael, Taylor, David, Tomino, Carlo, Torrent-Farnell, Josep, Upadhyaya, Sheela, Hutchings, Adam, Le Dez, Lugdivine
Publicado 2017