Real-World Clinical Outcomes Based on Body Mass Index and Annualized Weight Change in Patients with Idiopathic Pulmonary Fibrosis

por Lee, Joyce S., Martin-Schwarze, Adam, Freiheit, Elizabeth, Trzaskoma, Ben, Burg, Cindy
Publicado 2022

A phase IV, multicentre, open‐label study of emicizumab prophylaxis in people with haemophilia A with or without FVIII inhibitors undergoing minor surgical procedures

por Escobar, Miguel, Dunn, Amy, Quon, Doris, Trzaskoma, Ben, Lee, Lucy, Ko, Richard H., Carpenter, Shannon L.
Publicado 2022

Efficacy of emicizumab is maintained throughout dosing intervals for bleed prophylaxis

por Pipe, Steven W., Trzaskoma, Ben, Minhas, Miranda, Lehle, Michaela, Ko, Richard H., Gao, Ling, Mahlangu, Johnny, Kempton, Christine L., Kessler, Craig M., Kruse-Jarres, Rebecca
Publicado 2023

A Patient-Centered Evaluation of Meaningful Change on the 32-Item Motor Function Measure in Spinal Muscular Atrophy Using Qualitative and Quantitative Data

por Duong, Tina, Staunton, Hannah, Braid, Jessica, Barriere, Aurelie, Trzaskoma, Ben, Gao, Ling, Willgoss, Tom, Cruz, Rosangel, Gusset, Nicole, Gorni, Ksenija, Randhawa, Sharan, Yang, Lida, Vuillerot, Carole
Publicado 2022