Health‐related quality of life and caregiver burden of emicizumab in children with haemophilia A and factor VIII inhibitors—Results from the HAVEN 2 study

por Mancuso, Maria Elisa, Mahlangu, Johnny, Sidonio, Robert, Trask, Peter, Uguen, Marianne, Chang, Tiffany, Shima, Midori, Young, Guy, Oldenburg, Johannes, von Mackensen, Sylvia
Publicado 2020

Do pregnancies reduce iron overload in HFE hemochromatosis women? results from an observational prospective study

por Scotet, Virginie, Saliou, Philippe, Uguen, Marianne, L’Hostis, Carine, Merour, Marie-Christine, Triponey, Céline, Chanu, Brigitte, Nousbaum, Jean-Baptiste, Le Gac, Gerald, Ferec, Claude
Publicado 2018

Untreated bleeds in people with hemophilia A in a noninterventional study and intrapatient comparison after initiating emicizumab in HAVEN 1–3

por Callaghan, Michael U., Asikanius, Elina, Lehle, Michaela, Oldenburg, Johannes, Mahlangu, Johnny, Uguen, Marianne, Chebon, Sammy, Kruse‐Jarres, Rebecca, Jiménez‐Yuste, Víctor, Shima, Midori, Trask, Peter, Kempton, Christine L., Kessler, Craig M., Levy, Gallia G., Peyvandi, Flora
Publicado 2022

Safety and efficacy of zinpentraxin alfa as monotherapy or in combination with ruxolitinib in myelofibrosis: stage I of a phase II trial

por Verstovsek, Srdan, Foltz, Lynda, Gupta, Vikas, Hasserjian, Robert, Manshouri, Taghi, Mascarenhas, John, Mesa, Ruben, Pozdnyakova, Olga, Ritchie, Ellen, Veletic, Ivo, Gamel, Katia, Hamidi, Habib, Han, Lyrialle, Higgins, Brian, Trunzer, Kerstin, Uguen, Marianne, Wang, Dao, El-Galaly, Tarec Christoffer, Todorov, Boyan, Gotlib, Jason
Publicado 2023