Canine and Feline Models of Human Genetic Diseases and Their Contributions to Advancing Clinical Therapies


por Gurda, Brittney L., Bradbury, Allison M., Vite, Charles H.
Publicado 2017

Quantitative, noninvasive, in vivo longitudinal monitoring of gene expression in the brain by co-AAV transduction with a PET reporter gene

por Yoon, Sea Young, Gay-Antaki, Carlos, Ponde, Datta E, Poptani, Harish, Vite, Charles H, Wolfe, John H
Publicado 2014

Identification of the Rostral Migratory Stream in the Canine and Feline Brain

por Malik, Saafan Z., Lewis, Melissa, Isaacs, Alison, Haskins, Mark, Van Winkle, Thomas, Vite, Charles H., Watson, Deborah J.
Publicado 2012

A Homozygous MAN2B1 Missense Mutation in a Doberman Pinscher Dog with Neurodegeneration, Cytoplasmic Vacuoles, Autofluorescent Storage Granules, and an α-Mannosidase Deficiency

por Bullock, Garrett, Johnson, Gary S., Pattridge, Savannah G., Mhlanga-Mutangadura, Tendai, Guo, Juyuan, Cook, James, Campbell, Rebecca S., Vite, Charles H., Katz, Martin L.
Publicado 2023

Pharmacokinetics and distribution of 2‐hydroxypropyl‐β‐cyclodextrin following a single intrathecal dose to cats

por Kao, Mark L., Stellar, Susan, Solon, Eric, Lordi, Alfred, Kasica, Nicole, Swain, Gary, Bagel, Jessica H., Gurda, Brittney L., Vite, Charles H.
Publicado 2019

A Digital Atlas of the Dog Brain

por Datta, Ritobrato, Lee, Jongho, Duda, Jeffrey, Avants, Brian B., Vite, Charles H., Tseng, Ben, Gee, James C., Aguirre, Gustavo D., Aguirre, Geoffrey K.
Publicado 2012

Correction: A Digital Atlas of the Dog Brain

por Datta, Ritobrato, Lee, Jongho, Duda, Jeffrey, Avants, Brian B., Vite, Charles H., Tseng, Ben, Gee, James C., Aguirre, Gustavo D., Aguirre, Geoffrey K.
Publicado 2013

Widespread gene transfer in the central nervous system of cynomolgus macaques following delivery of AAV9 into the cisterna magna

por Hinderer, Christian, Bell, Peter, Vite, Charles H, Louboutin, Jean-Pierre, Grant, Rebecca, Bote, Erin, Yu, Hongwei, Pukenas, Bryan, Hurst, Robert, Wilson, James M
Publicado 2014

Pulmonary Abnormalities in Animal Models Due to Niemann-Pick Type C1 (NPC1) or C2 (NPC2) Disease

por Roszell, Blair R., Tao, Jian-Qin, Yu, Kevin J., Gao, Ling, Huang, Shaohui, Ning, Yue, Feinstein, Sheldon I., Vite, Charles H., Bates, Sandra R.
Publicado 2013

Fostering collaborative research for rare genetic disease: the example of niemann-pick type C disease

por Walkley, Steven U., Davidson, Cristin D., Jacoby, Jonathan, Marella, Philip D., Ottinger, Elizabeth A., Austin, Christopher P., Porter, Forbes D., Vite, Charles H., Ory, Daniel S.
Publicado 2016

Forecasting Seizures in Dogs with Naturally Occurring Epilepsy

por Howbert, J. Jeffry, Patterson, Edward E., Stead, S. Matt, Brinkmann, Ben, Vasoli, Vincent, Crepeau, Daniel, Vite, Charles H., Sturges, Beverly, Ruedebusch, Vanessa, Mavoori, Jaideep, Leyde, Kent, Sheffield, W. Douglas, Litt, Brian, Worrell, Gregory A.
Publicado 2014

Efficacy and Safety of a Krabbe Disease Gene Therapy

por Hordeaux, Juliette, Jeffrey, Brianne A., Jian, Jinlong, Choudhury, Gourav R., Michalson, Kristofer, Mitchell, Thomas W., Buza, Elizabeth L., Chichester, Jessica, Dyer, Cecilia, Bagel, Jessica, Vite, Charles H., Bradbury, Allison M., Wilson, James M.
Publicado 2022

Low incidence of hepatocellular carcinoma in mice and cats treated with systemic adeno-associated viral vectors

por Ferla, Rita, Alliegro, Marialuisa, Dell’Anno, Margherita, Nusco, Edoardo, Cullen, John M., Smith, Stephanie N., Wolfsberg, Tyra G., O’Donnell, Patricia, Wang, Ping, Nguyen, Anh-Dao, Chandler, Randy J., Chen, Zelin, Burgess, Shawn M., Vite, Charles H., Haskins, Mark E., Venditti, Charles P., Auricchio, Alberto
Publicado 2020

Defective Cytochrome P450-Catalysed Drug Metabolism in Niemann-Pick Type C Disease

por Nicoli, Elena-Raluca, Al Eisa, Nada, Cluzeau, Celine V. M., Wassif, Christopher A., Gray, James, Burkert, Kathryn R., Smith, David A., Morris, Lauren, Cologna, Stephanie M., Peer, Cody J., Sissung, Tristan M., Uscatu, Constantin-Daniel, Figg, William D., Pavan, William J., Vite, Charles H., Porter, Forbes D., Platt, Frances M.
Publicado 2016

Evaluation of AAV-mediated Gene Therapy for Central Nervous System Disease in Canine Mucopolysaccharidosis VII

por Gurda, Brittney L, De Guilhem De Lataillade, Adrien, Bell, Peter, Zhu, Yanqing, Yu, Hongwei, Wang, Ping, Bagel, Jessica, Vite, Charles H, Sikora, Tracey, Hinderer, Christian, Calcedo, Roberto, Yox, Alexander D, Steet, Richard A, Ruane, Therese, O'Donnell, Patricia, Gao, Guangping, Wilson, James M, Casal, Margret, Ponder, Katherine P, Haskins, Mark E
Publicado 2016