Self-cleaving guide RNAs enable pharmacological selection of precise gene editing events in vivo

por Tiyaboonchai, Amita, Vonada, Anne, Posey, Jeffrey, Pelz, Carl, Wakefield, Leslie, Grompe, Markus
Publicado 2022

Complete correction of murine phenylketonuria by selection-enhanced hepatocyte transplantation

por Vonada, Anne, Wakefield, Leslie, Martinez, Michael, Harding, Cary O., Grompe, Markus, Tiyaboonchai, Amita
Publicado 2023