Functional expression of Rab escort protein 1 following AAV2-mediated gene delivery in the retina of choroideremia mice and human cells ex vivo

por Tolmachova, Tanya, Tolmachov, Oleg E., Barnard, Alun R., de Silva, Samantha R., Lipinski, Daniel M., Walker, Nathan J., MacLaren, Robert E., Seabra, Miguel C.
Publicado 2013

Single residue AAV capsid mutation improves transduction of photoreceptors in the Abca4(-/-) mouse and bipolar cells in the rd1 mouse and human retina ex-vivo

por De Silva, Samantha R., Charbel Issa, Peter, Singh, Mandeep S., Lipinski, Daniel M., Barnea-Cramer, Alona O., Walker, Nathan J., Barnard, Alun R., Hankins, Mark W., MacLaren, Robert E.
Publicado 2016