In utero hematopoietic cell transplantation for hemoglobinopathies

por Derderian, S. Christopher, Jeanty, Cerine, Walters, Mark C., Vichinsky, Elliott, MacKenzie, Tippi C.
Publicado 2015

Thiol/Redox Metabolomic Profiling Implicates GSH Dysregulation in Early Experimental Graft versus Host Disease (GVHD)

por Suh, Jung H., Kanathezhath, Bindu, Shenvi, Swapna, Guo, Hua, Zhou, Alicia, Tiwana, Anureet, Kuypers, Frans, Ames, Bruce N., Walters, Mark C.
Publicado 2014

Dose-adapted post-transplant cyclophosphamide for HLA-haploidentical transplantation in Fanconi anemia

por Thakar, Monica S., Bonfim, Carmem, Walters, Mark C., Storb, Rainer, Pasquini, Ricardo, Burroughs, Lauri, Sandmaier, Brenda M., Woolfrey, Ann, Kiem, Hans-Peter
Publicado 2017

CRISPR-Cas9 interrogation of a putative fetal globin repressor in human erythroid cells

por Chung, Jennifer E., Magis, Wendy, Vu, Jonathan, Heo, Seok-Jin, Wartiovaara, Kirmo, Walters, Mark C., Kurita, Ryo, Nakamura, Yukio, Boffelli, Dario, Martin, David I. K., Corn, Jacob E., DeWitt, Mark A.
Publicado 2019

Lovo‐cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB‐206 study

por Kanter, Julie, Thompson, Alexis A., Pierciey, Francis J., Hsieh, Matthew, Uchida, Naoya, Leboulch, Philippe, Schmidt, Manfred, Bonner, Melissa, Guo, Ruiting, Miller, Alex, Ribeil, Jean‐Antoine, Davidson, David, Asmal, Mohammed, Walters, Mark C., Tisdale, John F.
Publicado 2022

High-level correction of the sickle mutation is amplified in vivo during erythroid differentiation

por Magis, Wendy, DeWitt, Mark A., Wyman, Stacia K., Vu, Jonathan T., Heo, Seok-Jin, Shao, Shirley J., Hennig, Finn, Romero, Zulema G., Campo-Fernandez, Beatriz, Said, Suzanne, McNeill, Matthew S., Rettig, Garrett R., Sun, Yongming, Wang, Yu, Behlke, Mark A., Kohn, Donald B., Boffelli, Dario, Walters, Mark C., Corn, Jacob E., Martin, David I.K.
Publicado 2022