Pregnancy outcome in women with Gaucher disease type 1 who had unplanned pregnancies during eliglustat clinical trials

por Lukina, Elena, Balwani, Manisha, Belmatoug, Nadia, Watman, Nora, Hughes, Derralynn, Gaemers, Sebastiaan J. M., Foster, Meredith C., Lewis, Grace, Peterschmitt, M. Judith
Publicado 2020

Outcomes after 8 years of eliglustat therapy for Gaucher disease type 1: Final results from the Phase 2 trial

por Lukina, Elena, Watman, Nora, Dragosky, Marta, Lau, Heather, Avila Arreguin, Elsa, Rosenbaum, Hanna, Zimran, Ari, Foster, Meredith C., Gaemers, Sebastiaan J. M., Peterschmitt, M. Judith
Publicado 2018

Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat

por Kamath, Ravi S., Lukina, Elena, Watman, Nora, Dragosky, Marta, Pastores, Gregory M., Arreguin, Elsa Avila, Rosenbaum, Hanna, Zimran, Ari, Aguzzi, Rasha, Puga, Ana Cristina, Norfleet, Andrea M., Peterschmitt, M. Judith, Rosenthal, Daniel I.
Publicado 2014