MYCN-amplified neuroblastoma maintains an aggressive and undifferentiated phenotype by deregulation of estrogen and NGF signaling

por Dzieran, Johanna, Rodriguez Garcia, Aida, Westermark, Ulrica Kristina, Henley, Aine Brigette, Eyre Sánchez, Elena, Träger, Catarina, Johansson, Henrik Johan, Lehtiö, Janne, Arsenian-Henriksson, Marie
Publicado 2018

Intravenous delivery of a chemically modified sulfamidase efficiently reduces heparan sulfate storage and brain pathology in mucopolysaccharidosis IIIA mice

por Gustavsson, Susanne, Ohlin Sjöström, Elisabet, Tjernberg, Agneta, Janson, Juliette, Westermark, Ulrica, Andersson, Tommy, Makower, Åsa, Arnelöf, Erik, Andersson, Gudrun, Svartengren, Jan, Ekholm, Carina, Svensson Gelius, Stefan
Publicado 2019

Ancestral lysosomal enzymes with increased activity harbor therapeutic potential for treatment of Hunter syndrome

por Hendrikse, Natalie M., Sandegren, Anna, Andersson, Tommy, Blomqvist, Jenny, Makower, Åsa, Possner, Dominik, Su, Chao, Thalén, Niklas, Tjernberg, Agneta, Westermark, Ulrica, Rockberg, Johan, Svensson Gelius, Stefan, Syrén, Per-Olof, Nordling, Erik
Publicado 2021