Rational Design of Short Locked Nucleic Acid-Modified 2′-O-Methyl Antisense Oligonucleotides for Efficient Exon-Skipping In Vitro

por Le, Bao T., Adams, Abbie M., Fletcher, Susan, Wilton, Stephen D., Veedu, Rakesh N.
Publicado 2017

Induction of revertant fibres in the mdx mouse using antisense oligonucleotides

por Fall, Abbie M, Johnsen, Russell, Honeyman, Kaite, Iversen, Pat, Fletcher, Susan, Wilton, Stephen D
Publicado 2006

Smart functional nucleic acid chimeras: Enabling tissue specific RNA targeting therapy

por Aaldering, Lukas J, Tayeb, Hossam, Krishnan, Shilpa, Fletcher, Susan, Wilton, Stephen D, Veedu, Rakesh N
Publicado 2015

Primary Nasal Epithelial Cells as a Surrogate Cell Culture Model for Type-II Alveolar Cells to Study ABCA-3 Deficiency

por Shaw, Nicole C., Kicic, Anthony, Fletcher, Sue, Wilton, Stephen D., Stick, Stephen M., Schultz, André
Publicado 2022

Antisense suppression of donor splice site mutations in the dystrophin gene transcript

por Fletcher, Sue, Meloni, Penny L, Johnsen, Russell D, Wong, Brenda L, Muntoni, Francesco, Wilton, Stephen D
Publicado 2013

Revertant Fibers in the mdx Murine Model of Duchenne Muscular Dystrophy: An Age- and Muscle-Related Reappraisal

por Pigozzo, Sarah R., Da Re, Lorena, Romualdi, Chiara, Mazzara, Pietro G., Galletta, Eva, Fletcher, Sue, Wilton, Stephen D., Vitiello, Libero
Publicado 2013