Estimating the Prevalence of Transthyretin Amyloid Cardiomyopathy in a Large In-Hospital Database in Japan

por Winburn, Ian, Ishii, Tomonori, Sumikawa, Takuma, Togo, Kanae, Yasunaga, Hideo
Publicado 2019

The impact of bleeding event frequency on health-related quality of life and work productivity outcomes in a European cohort of adults with haemophilia A: insights from the CHESS I...

por Young, Lisa, Chen, Yong, Alvir, José, Burke, Tom, Ferri Grazzi, Enrico, Winburn, Ian
Publicado 2023

Rationale for using centralized transduction inhibition assays in three phase 3 rAAV gene therapy clinical trials

por Schulz, Martin, Bashirians, George, Cheng, Seng H., Levy, Daniel I., Lundie, Mark, Wilcox, Lisa, Winburn, Ian, Somanathan, Suryanarayan
Publicado 2023

Examining patient and professional perspectives in the UK for gene therapy in haemophilia

por Woollacott, Ione, Morgan, George, Chowdary, Pratima, O'Hara, Jamie, Franks, Bethany, van Overbeeke, Eline, Dunn, Nicola, Michelsen, Sissel, Huys, Isabelle, Martin, Antony, Cawson, Matthew, Brownrigg, Jack, Winburn, Ian, Thomson, Jim
Publicado 2022