State of the art of rare disease activities around the world: overview of the non-European landscape

por Wong-Rieger, Durhane
Publicado 2012

Developing a Patient-Directed Policy Framework for Managing Orphan and Ultra-Orphan Drugs Throughout Their Lifecycle

por Menon, Devidas, Stafinski, Tania, Dunn, Andrea, Wong-Rieger, Durhane
Publicado 2015

Review of 11 national policies for rare diseases in the context of key patient needs

por Dharssi, Safiyya, Wong-Rieger, Durhane, Harold, Matthew, Terry, Sharon
Publicado 2017

An international comparative analysis of public reimbursement of orphan drugs in Canadian provinces compared to European countries

por Ward, Leanne Marie, Chambers, Alexandra, Mechichi, Emine, Wong-Rieger, Durhane, Campbell, Craig
Publicado 2022

Essential list of medicinal products for rare diseases: recommendations from the IRDiRC Rare Disease Treatment Access Working Group

por Gahl, William A., Wong-Rieger, Durhane, Hivert, Virginie, Yang, Rachel, Zanello, Galliano, Groft, Stephen
Publicado 2021

Returning incidental findings from genetic research to children: views of parents of children affected by rare diseases

por Kleiderman, Erika, Knoppers, Bartha Maria, Fernandez, Conrad V, Boycott, Kym M, Ouellette, Gail, Wong-Rieger, Durhane, Adam, Shelin, Richer, Julie, Avard, Denise
Publicado 2014

How can we deliver on the promise of precision medicine in oncology and beyond? A practical roadmap for action

por Baird, Anne‐Marie, Westphalen, C. Benedikt, Blum, Sandra, Nafria, Begonya, Knott, Tanya, Sargeant, Ify, Harnik, Helena, Brooke, Nicholas, Wicki, Nicole, Wong‐Rieger, Durhane
Publicado 2023

Model consent clauses for rare disease research

por Nguyen, Minh Thu, Goldblatt, Jack, Isasi, Rosario, Jagut, Marlene, Jonker, Anneliene Hechtelt, Kaufmann, Petra, Ouillade, Laetitia, Molnar-Gabor, Fruszina, Shabani, Mahsa, Sid, Eric, Tassé, Anne Marie, Wong-Rieger, Durhane, Knoppers, Bartha Maria
Publicado 2019

A call for action to improve access to care and treatment for patients with rare diseases in the Asia-Pacific region

por Soon, Swee-Sung, Lopes, Gilberto, Lim, Hwee-Yong, Wong-Rieger, Durhane, Bahri, Salmah, Hickinbotham, Lucy, Jha, Anand, Ko, Bor-Sheng, MacDonell, Diana, Pwu, Jasmine Roah-Fang, Shih, Ruby, Sirachainan, Ekaphop, Suh, Dong-Churl, Wale, Janet, Zhang, Xiao, Wee, Hwee-Lin
Publicado 2014

The IRDiRC Chrysalis Task Force: making rare disease research attractive to companies

por Beaverson, Katherine L., Julkowska, Daria, Letinturier, Mary Catherine V., Aartsma-Rus, Annemieke, Austin, Jennifer, Bueren, Juan, Frost, Simon, Hamamura, Misako, Larkindale, Jane, LaRosa, Greg, Magenheim, Rita, Merico, Annamaria, Gerdina Pasmooij, Anna Maria, Pirard, Vinciane, Ekow Thomford, Nicholas, Wada, Michihiko, Wong-Rieger, Durhane, Hartman, Adam L.
Publicado 2023

Personalizing health care: feasibility and future implications

por Godman, Brian, Finlayson, Alexander E, Cheema, Parneet K, Zebedin-Brandl, Eva, Gutiérrez-Ibarluzea, Inaki, Jones, Jan, Malmström, Rickard E, Asola, Elina, Baumgärtel, Christoph, Bennie, Marion, Bishop, Iain, Bucsics, Anna, Campbell, Stephen, Diogene, Eduardo, Ferrario, Alessandra, Fürst, Jurij, Garuoliene, Kristina, Gomes, Miguel, Harris, Katharine, Haycox, Alan, Herholz, Harald, Hviding, Krystyna, Jan, Saira, Kalaba, Marija, Kvalheim, Christina, Laius, Ott, Lööv, Sven-Ake, Malinowska, Kamila, Martin, Andrew, McCullagh, Laura, Nilsson, Fredrik, Paterson, Ken, Schwabe, Ulrich, Selke, Gisbert, Sermet, Catherine, Simoens, Steven, Tomek, Dominik, Vlahovic-Palcevski, Vera, Voncina, Luka, Wladysiuk, Magdalena, van Woerkom, Menno, Wong-Rieger, Durhane, Zara, Corrine, Ali, Raghib, Gustafsson, Lars L
Publicado 2013