Pre Clinical Assessment of AAVrh74.MCK.GNE Viral Vector Therapeutic Potential: Robust Activity Despite Lack of Consistent Animal Model for GNE Myopathy

por Mitrani-Rosenbaum, Stella, Yakovlev, Lena, Becker Cohen, Michal, Argov, Zohar, Fellig, Yakov, Harazi, Avi
Publicado 2022

In vivo and in vitro genome editing to explore GNE functions

por Ilouz, Nili, Harazi, Avi, Guttman, Miriam, Daya, Alon, Ruppo, Shmuel, Yakovlev, Lena, Mitrani-Rosenbaum, Stella
Publicado 2022

Upregulation of Hallmark Muscle Genes Protects Gne(M743T/M743T) Mutated Knock-In Mice From Kidney and Muscle Phenotype

por Benyamini, Hadar, Kling, Yehuda, Yakovlev, Lena, Becker Cohen, Michal, Nevo, Yuval, Elgavish, Sharona, Harazi, Avi, Argov, Zohar, Sela, Ilan, Mitrani-Rosenbaum, Stella
Publicado 2020