Gene-specific nonsense-mediated mRNA decay targeting for cystic fibrosis therapy

por Kim, Young Jin, Nomakuchi, Tomoki, Papaleonidopoulou, Foteini, Yang, Lucia, Zhang, Qian, Krainer, Adrian R.
Publicado 2022

Exon-skipping antisense oligonucleotides for cystic fibrosis therapy

por Kim, Young Jin, Sivetz, Nicole, Layne, Jessica, Voss, Dillon M., Yang, Lucia, Zhang, Qian, Krainer, Adrian R.
Publicado 2022

Identification of AAV serotypes for lung gene therapy in human embryonic stem cell-derived lung organoids

por Meyer-Berg, Helena, Zhou Yang, Lucia, Pilar de Lucas, María, Zambrano, Alberto, Hyde, Stephen C., Gill, Deborah R.
Publicado 2020

Chemical Replacement of Noggin with Dorsomorphin Homolog 1 for Cost-Effective Direct Neuronal Conversion

por Böhnke, Lena, Zhou-Yang, Lucia, Pelucchi, Silvia, Kogler, Flora, Frantal, Daniela, Schön, Florian, Lagerström, Stina, Borgogno, Oliver, Baltazar, Jennifer, Herdy, Joseph R., Kittel-Schneider, Sarah, Defrancesco, Michaela, Mertens, Jerome
Publicado 2022

Age-dependent instability of mature neuronal fate in induced neurons from Alzheimer’s patients

por Mertens, Jerome, Herdy, Joseph R., Traxler, Larissa, Schafer, Simon T., Schlachetzki, Johannes C.M., Böhnke, Lena, Reid, Dylan A., Lee, Hyungjun, Zangwill, Dina, Fernandes, Diana P., Agarwal, Ravi K., Lucciola, Raffaella, Zhou-Yang, Lucia, Karbacher, Lukas, Edenhofer, Frank, Stern, Shani, Horvath, Steve, Paquola, Apua C.M., Glass, Christopher K., Yuan, Shauna H., Ku, Manching, Szücs, Attila, Goldstein, Lawrence S.B., Galasko, Douglas, Gage, Fred H.
Publicado 2021