Induced Pluripotent Stem Cell Derivation and Ex Vivo Gene Correction Using a Mucopolysaccharidosis Type 1 Disease Mouse Model

por Miki, Toshio, Vazquez, Ludivina, Yanuaria, Lisa, Lopez, Omar, Garcia, Irving M., Ohashi, Kazuo, Rodriguez, Natalie S.
Publicado 2019

Liver‐Directed Human Amniotic Epithelial Cell Transplantation Improves Systemic Disease Phenotype in Hurler Syndrome Mouse Model

por Rodriguez, Natalie S., Yanuaria, Lisa, Parducho, Kevin Murphy R., Garcia, Irving M., Varghese, Bino A., Grubbs, Brendan H., Miki, Toshio
Publicado 2017