Mutant torsinA in the heterozygous DYT1 state compromises HSV propagation in infected neurons and fibroblasts

por György, Bence, Cruz, Lilian, Yellen, David, Aufiero, Massimo, Alland, Isabel, Zhang, Xuan, Ericsson, Maria, Fraefel, Cornel, Li, Yu-Ching, Takeda, Shuko, Hyman, Bradley T., Breakefield, Xandra O.
Publicado 2018

Gene therapy for tuberous sclerosis complex type 2 in a mouse model by delivery of AAV9 encoding a condensed form of tuberin

por Cheah, Pike-See, Prabhakar, Shilpa, Yellen, David, Beauchamp, Roberta L., Zhang, Xuan, Kasamatsu, Shingo, Bronson, Roderick T., Thiele, Elizabeth A., Kwiatkowski, David J., Stemmer-Rachamimov, Anat, György, Bence, Ling, King-Hwa, Kaneki, Masao, Tannous, Bakhos A., Ramesh, Vijaya, Maguire, Casey A., Breakefield, Xandra O.
Publicado 2021