Developing interactions with industry in rare diseases: lessons learned and continuing challenges

por Berry, Susan A., Coughlin, Curtis R., McCandless, Shawn, McCarter, Robert, Seminara, Jennifer, Yudkoff, Mark, LeMons, Cynthia
Publicado 2019

Conducting an investigator-initiated randomized double-blinded intervention trial in acute decompensation of inborn errors of metabolism: Lessons from the N-Carbamylglutamate Conso...

por Ah Mew, Nicholas, Cnaan, Avital, McCarter, Robert, Choi, Henry, Glass, Penny, Rice, Katie, Scavo, Louis, Gillespie, Catherine W., Diaz, George A., Berry, Gerard T., Wong, Derek, Konczal, Laura, McCandless, Shawn E., Coughlin II, Curtis R., Weisfeld-Adams, James D., Ficicioglu, Can, Yudkoff, Mark, Enns, Gregory M., Lichter-Konecki, Uta, Gallagher, Renata, Tuchman, Mendel
Publicado 2018