Improved cell metabolism prolongs photoreceptor survival upon retinal-pigmented epithelium loss in the sodium iodate induced model of geographic atrophy

por Zieger, Marina, Punzo, Claudio
Publicado 2016

CX3CL1 (Fractalkine) Protein Expression in Normal and Degenerating Mouse Retina: In Vivo Studies

por Zieger, Marina, Ahnelt, Peter K., Uhrin, Pavel
Publicado 2014

Muscle-Directed Delivery of an AAV1 Vector Leads to Capsid-Specific T Cell Exhaustion in Nonhuman Primates and Humans

por Gernoux, Gwladys, Gruntman, Alisha M., Blackwood, Meghan, Zieger, Marina, Flotte, Terence R., Mueller, Christian
Publicado 2020

Aerobic Glycolysis Is Essential for Normal Rod Function and Controls Secondary Cone Death in Retinitis Pigmentosa

por Petit, Lolita, Ma, Shan, Cipi, Joris, Cheng, Shun-Yun, Zieger, Marina, Hay, Nissim, Punzo, Claudio
Publicado 2018

Liver-directed SERPINA1 gene therapy attenuates progression of spontaneous and tobacco smoke-induced emphysema in α1-antitrypsin null mice

por Zieger, Marina, Borel, Florie, Greer, Cynthia, Gernoux, Gwladys, Blackwood, Meghan, Flotte, Terence R., Mueller, Christian
Publicado 2022

Intralingual and Intrapleural AAV Gene Therapy Prolongs Survival in a SOD1 ALS Mouse Model

por Keeler, Allison M., Zieger, Marina, Semple, Carson, Pucci, Logan, Veinbachs, Alessandra, Brown, Robert H., Mueller, Christian, ElMallah, Mai K.
Publicado 2019

Editing out five Serpina1 paralogs to create a mouse model of genetic emphysema

por Borel, Florie, Sun, Huaming, Zieger, Marina, Cox, Andrew, Cardozo, Brynn, Li, Weiying, Oliveira, Gabriella, Davis, Airiel, Gruntman, Alisha, Flotte, Terence R., Brodsky, Michael H., Hoffman, Andrew M., Elmallah, Mai K., Mueller, Christian
Publicado 2018

Precise therapeutic gene correction by a simple nuclease-induced double-strand break

por Iyer, Sukanya, Suresh, Sneha, Guo, Dongsheng, Daman, Katelyn, Chen, Jennifer C. J., Liu, Pengpeng, Zieger, Marina, Luk, Kevin, Roscoe, Benjamin P., Mueller, Christian, King, Oliver D., Emerson, Charles P., Wolfe, Scot A.
Publicado 2019