Regulatory-Compliant Validation of a Highly Sensitive qPCR for Biodistribution Assessment of Hemophilia A Patient Cells

por Bittorf, Patrick, Bergmann, Thorsten, Merlin, Simone, Olgasi, Cristina, Pullig, Oliver, Sanzenbacher, Ralf, Zierau, Martin, Walles, Heike, Follenzi, Antonia, Braspenning, Joris
Publicado 2020

Efficient and safe correction of hemophilia A by lentiviral vector-transduced BOECs in an implantable device

por Olgasi, Cristina, Borsotti, Chiara, Merlin, Simone, Bergmann, Thorsten, Bittorf, Patrick, Adewoye, Adeolu Badi, Wragg, Nicholas, Patterson, Kelcey, Calabria, Andrea, Benedicenti, Fabrizio, Cucci, Alessia, Borchiellini, Alessandra, Pollio, Berardino, Montini, Eugenio, Mazzuca, Delfina M., Zierau, Martin, Stolzing, Alexandra, Toleikis, Philip.M., Braspenning, Joris, Follenzi, Antonia
Publicado 2021